The TREAT-NMD Duchenne Muscular Dystrophy Registries: Conception, Design, and Utilization by Industry and Academia

Corticosteroids in Duchenne muscular dystrophy: Major variations in practice

(2013) Robert C. Griggs et al.   MUSCLE & NERVE

Can outcomes in Duchenne muscular dystrophy be improved by public reporting of data?

(2013) M. A. Scully et al.   NEUROLOGY

Advances in therapeutic RNA-targeting

(2013) Gert-Jan B. van Ommen et al.   New Biotechnology

Characteristics of Japanese Duchenne and Becker muscular dystrophy patients in a novel Japanese national registry of muscular dystrophy (Remudy)

(2013) Harumasa Nakamura et al.   Orphanet Journal of Rare Diseases

The New Zealand Neuromuscular Disease Registry

(2012) Miriam Rodrigues et al.   JOURNAL OF CLINICAL NEUROSCIENCE

TREAT-NMD workshop: Pattern recognition in genetic muscle diseases using muscle MRI

(2012) Volker Straub et al.   NEUROMUSCULAR DISORDERS

Towards harmonization of protocols for MRI outcome measures in skeletal muscle studies: Consensus recommendations from two TREAT-NMD NMR workshops, 2 May 2010, Stockholm, Sweden, 1–2 October 2009, Paris, France

(2012) Kieren G. Hollingsworth et al.   NEUROMUSCULAR DISORDERS

Novel Approaches to Corticosteroid Treatment in Duchenne Muscular Dystrophy

(2012) Eric P. Hoffman et al.   Physical Medicine and Rehabilitation Clinics of North America

Motor and respiratory heterogeneity in Duchenne patients: Implication for clinical trials

(2011) Véronique Humbertclaude et al.   EUROPEAN JOURNAL OF PAEDIATRIC NEUROLOGY

Duchenne Muscular Dystrophy: A 30-Year Population-Based Incidence Study

(2010) Joseph Dooley et al.   CLINICAL PEDIATRICS

Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations

(2009) Annemieke Aartsma-Rus et al.   HUMAN MUTATION

Genotype-phenotype analysis in 2,405 patients with a dystrophinopathy using the UMD-DMD database: a model of nationwide knowledgebase

(2009) Sylvie Tuffery-Giraud et al.   HUMAN MUTATION

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

(2009) Katharine Bushby et al.   LANCET NEUROLOGY

Characterization of the DMD/BMD patient population in Czech Republic and Slovakia using an innovative registry approach

(2009) Petr Brabec et al.   NEUROMUSCULAR DISORDERS

Mutation Analysis in a Population-Based Cohort of Boys With Duchenne or Becker Muscular Dystrophy

(2008) Christopher Cunniff et al.   JOURNAL OF CHILD NEUROLOGY

Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; Report of three expert workshops: TREAT-NMD/ENMC Workshop on outcome measures, 12th–13th May 2007, Naarden, The Netherlands; TREAT-NMD Workshop on outcome measures in experimental trials for DMD, 30th June–1st July 2007, Naarden, The Netherlands; Conjoint Institute of Myology TREAT-NMD Meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France

(2008) E. Mercuri et al.   NEUROMUSCULAR DISORDERS

157th ENMC International Workshop: Patient registries for rare, inherited muscular disorders 25–27 January 2008 Naarden, The Netherlands

(2008) Anna Sárközy et al.   NEUROMUSCULAR DISORDERS