Characteristics of Japanese Duchenne and Becker muscular dystrophy patients in a novel Japanese national registry of muscular dystrophy (Remudy)

China's first rare-disease registry is under development

(2011) Yan-Jun Zhang et al.   LANCET

Systemic Administration of PRO051 in Duchenne's Muscular Dystrophy

(2011) Nathalie M. Goemans et al.   NEW ENGLAND JOURNAL OF MEDICINE

Molecular treatments in Duchenne muscular dystrophy

(2010) Michela Guglieri et al.   CURRENT OPINION IN PHARMACOLOGY

Mutation spectrum of the dystrophin gene in 442 Duchenne/Becker muscular dystrophy cases from one Japanese referral center

(2010) Yasuhiro Takeshima et al.   JOURNAL OF HUMAN GENETICS

Duchenne muscular dystrophy: Survival by cardio-respiratory interventions

(2010) Yuka Ishikawa et al.   NEUROMUSCULAR DISORDERS

Patient Registries and Trial Readiness in Myotonic Dystrophy – TREAT-NMD/Marigold International Workshop Report

(2009) Rachel Thompson et al.   NEUROMUSCULAR DISORDERS