标题
Cyclodextrins applied to the treatment of lysosomal storage disorders
作者
关键词
-
出版物
ADVANCED DRUG DELIVERY REVIEWS
Volume 191, Issue -, Pages 114617
出版商
Elsevier BV
发表日期
2022-11-08
DOI
10.1016/j.addr.2022.114617
参考文献
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注意:仅列出部分参考文献,下载原文获取全部文献信息。- Inclusion Solves Insolubility —Translational Research Cycle from Bedside to Bench and Bench to Bedside for Drug Development Targeting Niemann-Pick Disease Type C—
- (2022) Tetsumi Irie YAKUGAKU ZASSHI-JOURNAL OF THE PHARMACEUTICAL SOCIETY OF JAPAN
- Current treatment options and novel nanotechnology-driven enzyme replacement strategies for lysosomal storage disorders
- (2022) Ambra Del Grosso et al. ADVANCED DRUG DELIVERY REVIEWS
- Intracerebroventricular Treatment with 2-Hydroxypropyl-β-Cyclodextrin Decreased Cerebellar and Hepatic Glycoprotein Nonmetastatic Melanoma Protein B (GPNMB) Expression in Niemann–Pick Disease Type C Model Mice
- (2021) Madoka Fukaura et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Gender-Specific Effects of Two Treatment Strategies in a Mouse Model of Niemann-Pick Disease Type C1
- (2021) Carsten Holzmann et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Differential mode of cholesterol inclusion with 2‐hydroxypropyl‐cyclodextrins increases safety margin in treatment of Niemann‐Pick disease type C
- (2021) Yusei Yamada et al. BRITISH JOURNAL OF PHARMACOLOGY
- Lipid-mediated motor-adaptor sequestration impairs axonal lysosome delivery leading to autophagic stress and dystrophy in Niemann-Pick type C
- (2021) Joseph C. Roney et al. DEVELOPMENTAL CELL
- Fabry Disease: The Current Treatment Landscape
- (2021) Malte Lenders et al. DRUGS
- One-year results of a clinical trial of olipudase alfa enzyme replacement therapy in pediatric patients with acid sphingomyelinase deficiency
- (2021) George A. Diaz et al. GENETICS IN MEDICINE
- Transcriptome of HPβCD-treated Niemann-pick disease type C1 cells highlights GPNMB as a biomarker for therapeutics
- (2021) Jorge L Rodriguez-Gil et al. HUMAN MOLECULAR GENETICS
- Estimating the prevalence of Niemann-Pick disease type C (NPC) in the United States
- (2021) Barbara K. Burton et al. MOLECULAR GENETICS AND METABOLISM
- Spatiotemporal Developmental Upregulation of Prestin Correlates With the Severity and Location of Cyclodextrin-Induced Outer Hair Cell Loss and Hearing Loss
- (2021) Dalian Ding et al. Frontiers in Cell and Developmental Biology
- A human iPSC-derived inducible neuronal model of Niemann-Pick disease, type C1
- (2021) Anika V. Prabhu et al. BMC BIOLOGY
- Acid Sphingomyelinase Deficiency: A Clinical and Immunological Perspective
- (2021) Carolina Pinto et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trial
- (2021) Jordi Diaz-Manera et al. LANCET NEUROLOGY
- Glial contribution to cyclodextrin-mediated reversal of cholesterol accumulation in murine NPC1-deficient neurons in vivo
- (2021) Amélie Barthelemy et al. NEUROBIOLOGY OF DISEASE
- Differential Effects of 2-Hydroxypropyl-Cyclodextrins on Lipid Accumulation in Npc1-Null Cells
- (2020) Sanzana Hoque et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Nanoparticles containing β‐cyclodextrin potentially useful for the treatment of Niemann‐Pick C
- (2020) Bruna Donida et al. JOURNAL OF INHERITED METABOLIC DISEASE
- Monitoring the itinerary of lysosomal cholesterol in Niemann-Pick Type C1-deficient cells after cyclodextrin treatment
- (2020) McKenna Feltes et al. JOURNAL OF LIPID RESEARCH
- Abnormal LAMP1 glycosylation may play a role in Niemann-Pick disease, type C pathology
- (2020) Niamh X. Cawley et al. PLoS One
- Inherited disorders of lysosomal membrane transporters
- (2020) Marjan Huizing et al. BIOCHIMICA ET BIOPHYSICA ACTA-BIOMEMBRANES
- 2-Hydroxypropyl-gamma-cyclodextrin overcomes NPC1 deficiency by enhancing lysosome-ER association and autophagy
- (2020) Ashutosh Singhal et al. Scientific Reports
- Identification of Brain-Specific Treatment Effects in NPC1 Disease by Focusing on Cellular and Molecular Changes of Sphingosine-1-Phosphate Metabolism
- (2020) Anne Gläser et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Long-term efficacy of olipudase alfa in adults with acid sphingomyelinase deficiency (ASMD): Further clearance of hepatic sphingomyelin is associated with additional improvements in pro- and anti-atherogenic lipid profiles after 42 months of treatment
- (2020) Beth L. Thurberg et al. MOLECULAR GENETICS AND METABOLISM
- 2-Hydroxypropyl-β-cyclodextrin Ototoxicity in Adult Rats: Rapid Onset and Massive Destruction of Both Inner and Outer Hair Cells Above a Critical Dose
- (2020) Xiaopeng Liu et al. NEUROTOXICITY RESEARCH
- Investigating the Mechanism of Cyclodextrins in the Treatment of Niemann‐Pick Disease Type C Using Crosslinked 2‐Hydroxypropyl‐β‐cyclodextrin
- (2020) Dario Carradori et al. Small
- Lactose-appended β-cyclodextrin as an effective nanocarrier for brain delivery
- (2020) Ryoma Yokoyama et al. JOURNAL OF CONTROLLED RELEASE
- Application of a glycinated bile acid biomarker for diagnosis and assessment of response to treatment in Niemann-pick disease type C1
- (2020) Rohini Sidhu et al. MOLECULAR GENETICS AND METABOLISM
- Delineation of metabolic responses of Npc1 mice lacking the cholesterol-esterifying enzyme SOAT2 to acute treatment with 2-hydroxypropyl-β-cyclodextrin
- (2020) Charina M. Ramirez et al. STEROIDS
- In Vitro and In Vivo Evaluation of 6-O-α-Maltosyl-β-Cyclodextrin as a Potential Therapeutic Agent Against Niemann-Pick Disease Type C
- (2019) Nushrat Yasmin et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Treating Lysosomal Storage Disorders: What Have We Learnt?
- (2019) Robin H Lachmann JOURNAL OF INHERITED METABOLIC DISEASE
- In vivo Efficacy and Safety Evaluation of Lactosyl-β-cyclodextrin as a Therapeutic Agent for Hepatomegaly in Niemann-Pick Type C Disease
- (2019) Yuki Maeda et al. Nanomaterials
- Ontogenesis and Modulation of Intestinal Unesterified Cholesterol Sequestration in a Mouse Model of Niemann–Pick C1 Disease
- (2019) Adam M. Lopez et al. DIGESTIVE DISEASES AND SCIENCES
- A therapy with miglustat, 2-hydroxypropyl-ß-cyclodextrin and allopregnanolone restores splenic cholesterol homeostasis in Niemann-pick disease type C1
- (2019) Anna-Maria Neßlauer et al. Lipids in Health and Disease
- Expanded access with intravenous hydroxypropyl-β-cyclodextrin to treat children and young adults with Niemann-Pick disease type C1: a case report analysis
- (2019) Caroline Hastings et al. Orphanet Journal of Rare Diseases
- Cyclodextrin polymer improves atherosclerosis therapy and reduces ototoxicity
- (2019) Heegon Kim et al. JOURNAL OF CONTROLLED RELEASE
- Role of 6- O -α-maltosyl-β-cyclodextrin in lysosomal cholesterol deprivation in Npc1- deficient Chinese hamster ovary cells
- (2018) Yasuyo Okada et al. CARBOHYDRATE RESEARCH
- In Niemann-Pick C1 mouse models, glial-only expression of the normal gene extends survival much further than do changes in genetic background or treatment with hydroxypropyl-beta-cyclodextrin
- (2018) Craig A. Marshall et al. GENE
- Microglia activation in Niemann–Pick disease, type C1 is amendable to therapeutic intervention
- (2018) Antony Cougnoux et al. HUMAN MOLECULAR GENETICS
- Evaluation of Two Liver Treatment Strategies in a Mouse Model of Niemann–Pick-Disease Type C1
- (2018) Lynn Ebner et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- A pilot study of direct delivery of hydroxypropyl-beta-cyclodextrin to the lung by the nasal route in a mouse model of Niemann-Pick C1 disease: motor performance is unaltered and lung disease is worsened
- (2018) Robert P. Erickson et al. JOURNAL OF APPLIED GENETICS
- Polyrotaxane-based systemic delivery of β-cyclodextrins for potentiating therapeutic efficacy in a mouse model of Niemann-Pick type C disease
- (2018) Atsushi Tamura et al. JOURNAL OF CONTROLLED RELEASE
- LC3 Immunostaining in the Inferior Olivary Nuclei of Cats With Niemann-Pick Disease Type C1 Is Associated With Patterned Purkinje Cell Loss
- (2018) Brittney L Gurda et al. JOURNAL OF NEUROPATHOLOGY AND EXPERIMENTAL NEUROLOGY
- Predicting the Binding Mode of 2-Hydroxypropyl-β-cyclodextrin to Cholesterol by Means of the MD Simulation and the 3D-RISM-KH Theory
- (2018) Yuji Hayashino et al. JOURNAL OF PHYSICAL CHEMISTRY B
- Cyclodextrins: Assessing the Impact of Cavity Size, Occupancy, and Substitutions on Cytotoxicity and Cholesterol Homeostasis
- (2018) Lajos Szente et al. MOLECULES
- Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-β-Cyclodextrin
- (2018) Elizabeth Berry-Kravis et al. PEDIATRIC NEUROLOGY
- Linear Cyclodextrin Polymer Prodrugs as Novel Therapeutics for Niemann-Pick Type C1 Disorder
- (2018) Aditya Kulkarni et al. Scientific Reports
- The susceptibility of cochlear outer hair cells to cyclodextrin is not related to their electromotile activity
- (2018) Yingjie Zhou et al. Acta Neuropathologica Communications
- Main Olfactory and Vomeronasal Epithelium Are Differently Affected in Niemann-Pick Disease Type C1
- (2018) Martin Witt et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Necroptosis inhibition as a therapy for Niemann-Pick disease, type C1: Inhibition of RIP kinases and combination therapy with 2-hydroxypropyl-β-cyclodextrin
- (2018) A. Cougnoux et al. MOLECULAR GENETICS AND METABOLISM
- Hydroxypropyl-beta and -gamma cyclodextrins rescue cholesterol accumulation in Niemann–Pick C1 mutant cell via lysosome-associated membrane protein 1
- (2018) Ashutosh Singhal et al. Cell Death & Disease
- Shortened primary cilium length and dysregulated Sonic hedgehog signaling in Niemann-Pick C1 disease
- (2017) Sonia Canterini et al. HUMAN MOLECULAR GENETICS
- Increased Regenerative Capacity of the Olfactory Epithelium in Niemann–Pick Disease Type C1
- (2017) Anja Meyer et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Impact of the Niemann–Pick c1 Gene Mutation on the Total Cellular Glycomics of CHO Cells
- (2017) Jun-ichi Furukawa et al. JOURNAL OF PROTEOME RESEARCH
- Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological disease progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1–2 trial
- (2017) Daniel S Ory et al. LANCET
- Early experience with compassionate use of 2 hydroxypropyl-beta-cyclodextrin for Niemann–Pick type C disease: review of initial published cases
- (2017) Juan Eduardo Megías-Vericat et al. NEUROLOGICAL SCIENCES
- Neural stem cells for disease modeling of Wolman disease and evaluation of therapeutics
- (2017) Francis Aguisanda et al. Orphanet Journal of Rare Diseases
- Cyclodextrins and Iatrogenic Hearing Loss: New Drugs with Significant Risk
- (2017) Mark A. Crumling et al. Frontiers in Cellular Neuroscience
- Characterization of hydroxypropyl-beta-cyclodextrins used in the treatment of Niemann-Pick Disease type C1
- (2017) Alfred L. Yergey et al. PLoS One
- Direct administration of 2-Hydroxypropyl-Beta-Cyclodextrin into guinea pig cochleae: Effects on physiological and histological measurements
- (2017) J. T. Lichtenhan et al. PLoS One
- Noise-Induced Loss of Hair Cells and Cochlear Synaptopathy Are Mediated by the Activation of AMPK
- (2016) K. Hill et al. JOURNAL OF NEUROSCIENCE
- Reversal of Pathologic Lipid Accumulation in NPC1-Deficient Neurons by Drug-Promoted Release of LAMP1-Coated Lamellar Inclusions
- (2016) Valérie Demais et al. JOURNAL OF NEUROSCIENCE
- In vitro evaluation of 2-hydroxyalkylated β-cyclodextrins as potential therapeutic agents for Niemann-Pick Type C disease
- (2016) Yuki Kondo et al. MOLECULAR GENETICS AND METABOLISM
- Lysosomal pH-inducible supramolecular dissociation of polyrotaxanes possessing acid-labile N-triphenylmethyl end groups and their therapeutic potential for Niemann-Pick type C disease
- (2016) Atsushi Tamura et al. SCIENCE AND TECHNOLOGY OF ADVANCED MATERIALS
- PEG-lipid micelles enable cholesterol efflux in Niemann-Pick Type C1 disease-based lysosomal storage disorder
- (2016) Anna Brown et al. Scientific Reports
- Induced Pluripotent Stem Cells for Disease Modeling and Evaluation of Therapeutics for Niemann-Pick Disease Type A
- (2016) Yan Long et al. Stem Cells Translational Medicine
- Efficacy and ototoxicity of different cyclodextrins in Niemann-Pick C disease
- (2016) Cristin D. Davidson et al. Annals of Clinical and Translational Neurology
- Developmental delay in motor skill acquisition in Niemann-Pick C1 mice reveals abnormal cerebellar morphogenesis
- (2016) Paola Caporali et al. Acta Neuropathologica Communications
- Susceptibility of outer hair cells to cholesterol chelator 2-hydroxypropyl-β-cyclodextrine is prestin-dependent
- (2016) Satoe Takahashi et al. Scientific Reports
- Cholesterol lowering effects of mono-lactose-appended β-cyclodextrin in Niemann–Pick type C disease-like HepG2 cells
- (2015) Keiichi Motoyama et al. Beilstein Journal of Organic Chemistry
- Efficacy of 2-Hydroxypropyl-β-cyclodextrin in Niemann–Pick Disease Type C Model Mice and Its Pharmacokinetic Analysis in a Patient with the Disease
- (2015) Yuta Tanaka et al. BIOLOGICAL & PHARMACEUTICAL BULLETIN
- Immunogenicity of Elosulfase Alfa, an Enzyme Replacement Therapy in Patients With Morquio A Syndrome: Results From MOR-004, a Phase III Trial
- (2015) Becky Schweighardt et al. CLINICAL THERAPEUTICS
- Enhanced delivery of daidzein into fibroblasts and neuronal cells with cationic derivatives of gamma-cyclodextrin for the control of cellular glycosaminoglycans
- (2015) Kamil Kamiński et al. EUROPEAN JOURNAL OF PHARMACEUTICS AND BIOPHARMACEUTICS
- BCM-95 and (2-hydroxypropyl)-β-cyclodextrin reverse autophagy dysfunction and deplete stored lipids in Sap C-deficient fibroblasts
- (2015) Massimo Tatti et al. HUMAN MOLECULAR GENETICS
- Hearing Loss and Otopathology Following Systemic and Intracerebroventricular Delivery of 2-Hydroxypropyl-Beta-Cyclodextrin
- (2015) Scott Cronin et al. JARO-JOURNAL OF THE ASSOCIATION FOR RESEARCH IN OTOLARYNGOLOGY
- β-Cyclodextrin-threaded Biocleavable Polyrotaxanes Ameliorate Impaired Autophagic Flux in Niemann-Pick Type C Disease
- (2015) Atsushi Tamura et al. JOURNAL OF BIOLOGICAL CHEMISTRY
- Effects of cyclodextrins on GM1-gangliosides in fibroblasts from GM1-gangliosidosis patients
- (2015) Yuki Maeda et al. JOURNAL OF PHARMACY AND PHARMACOLOGY
- Intrathecal 2-Hydroxypropyl-Beta-Cyclodextrin (HPBCD) therapy in adult-onset Niemann-Pick Disease Type C (NPC)
- (2015) Y. Sakiyama et al. JOURNAL OF THE NEUROLOGICAL SCIENCES
- Intrathecal 2-hydroxypropyl-beta-cyclodextrin in a single patient with Niemann–Pick C1
- (2015) Timothy J. Maarup et al. MOLECULAR GENETICS AND METABOLISM
- How to reduce the accumulation of autophagic vacuoles in NPC1-deficient neurons: A comparison of two pharmacological strategies
- (2015) Volker Meske et al. NEUROPHARMACOLOGY
- A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency
- (2015) Barbara K. Burton et al. NEW ENGLAND JOURNAL OF MEDICINE
- Visual evoked potentials of Niemann-Pick type C1 mice reveal an impairment of the visual pathway that is rescued by 2-hydroxypropyl-ß-cyclodextrin
- (2015) Giampiero Palladino et al. Orphanet Journal of Rare Diseases
- Intracisternal cyclodextrin prevents cerebellar dysfunction and Purkinje cell death in feline Niemann-Pick type C1 disease
- (2015) Charles H. Vite et al. Science Translational Medicine
- HPGCD Outperforms HPBCD as a Potential Treatment for Niemann-Pick Disease Type C During Disease Modeling with iPS Cells
- (2015) Minami Soga et al. STEM CELLS
- Cyclodextrins, Blood–Brain Barrier, and Treatment of Neurological Diseases
- (2014) Miklós Vecsernyés et al. ARCHIVES OF MEDICAL RESEARCH
- Plasma Signature of Neurological Disease in the Monogenetic Disorder Niemann-Pick Type C
- (2014) Md. Suhail Alam et al. JOURNAL OF BIOLOGICAL CHEMISTRY
- Complex lipid trafficking in Niemann-Pick disease type C
- (2014) Marie T. Vanier JOURNAL OF INHERITED METABOLIC DISEASE
- Reduced cerebellar neurodegeneration after combined therapy with cyclodextrin/allopregnanolone and miglustat in NPC1: A mouse model of Niemann-Pick type C1 disease
- (2014) Fabian Maass et al. JOURNAL OF NEUROSCIENCE RESEARCH
- The autophagic defect in Niemann–Pick disease type C neurons differs from somatic cells and reduces neuronal viability
- (2014) Volker Meske et al. NEUROBIOLOGY OF DISEASE
- A marked paucity of granule cells in the developing cerebellum of the Npc1−/− mouse is corrected by a single injection of hydroxypropyl-β-cyclodextrin
- (2014) S. Nusca et al. NEUROBIOLOGY OF DISEASE
- Targeted delivery of pharmacological chaperones for Gaucher disease to macrophages by a mannosylated cyclodextrin carrier
- (2014) Julio Rodríguez-Lavado et al. ORGANIC & BIOMOLECULAR CHEMISTRY
- Lysosomal-specific Cholesterol Reduction by Biocleavable Polyrotaxanes for Ameliorating Niemann-Pick Type C Disease
- (2014) Atsushi Tamura et al. Scientific Reports
- Genetic and Chemical Correction of Cholesterol Accumulation and Impaired Autophagy in Hepatic and Neural Cells Derived from Niemann-Pick Type C Patient-Specific iPS Cells
- (2014) Dorothea Maetzel et al. Stem Cell Reports
- Auditory Phenotype of Niemann-Pick Disease, Type C1
- (2013) Kelly A. King et al. EAR AND HEARING
- Galsulfase (Naglazyme®) therapy in infants with mucopolysaccharidosis VI
- (2013) Paul R. Harmatz et al. JOURNAL OF INHERITED METABOLIC DISEASE
- Identification of Niemann-Pick C1 disease biomarkers through sphingolipid profiling
- (2013) Martin Fan et al. JOURNAL OF LIPID RESEARCH
- Gangliosides and Gangliosidoses: Principles of Molecular and Metabolic Pathogenesis
- (2013) K. Sandhoff et al. JOURNAL OF NEUROSCIENCE
- Lung toxicity of hydroxypropyl-β-cyclodextrin infusion
- (2013) Yin-Hsiu Chien et al. MOLECULAR GENETICS AND METABOLISM
- Combined therapy with cyclodextrin/allopregnanolone and miglustat improves motor but not cognitive functions in Niemann–Pick Type C1 mice
- (2013) M. Hovakimyan et al. NEUROSCIENCE
- Impaired Autophagy in the Lipid-Storage Disorder Niemann-Pick Type C1 Disease
- (2013) Sovan Sarkar et al. Cell Reports
- Microarray expression analysis and identification of serum biomarkers for Niemann–Pick disease, type C1
- (2012) Celine V.M. Cluzeau et al. HUMAN MOLECULAR GENETICS
- Mutant human APP exacerbates pathology in a mouse model of NPC and its reversal by a β-cyclodextrin
- (2012) Mahua Maulik et al. HUMAN MOLECULAR GENETICS
- Normalization of Cholesterol Homeostasis by 2-Hydroxypropyl-β-cyclodextrin in Neurons and Glia from Niemann-Pick C1 (NPC1)-deficient Mice
- (2012) Kyle B. Peake et al. JOURNAL OF BIOLOGICAL CHEMISTRY
- Cyclodextrin mediates rapid changes in lipid balance inNpc1−/−mice without carrying cholesterol through the bloodstream
- (2012) Anna M. Taylor et al. JOURNAL OF LIPID RESEARCH
- Amyloid-β metabolism in Niemann-Pick C disease models and patients
- (2012) Niklas Mattsson et al. METABOLIC BRAIN DISEASE
- Recommendations for the diagnosis and management of Niemann–Pick disease type C: An update
- (2012) Marc C. Patterson et al. MOLECULAR GENETICS AND METABOLISM
- Effects of cyclodextrin in two patients with Niemann–Pick Type C disease
- (2012) Muneaki Matsuo et al. MOLECULAR GENETICS AND METABOLISM
- Hearing Loss and Hair Cell Death in Mice Given the Cholesterol-Chelating Agent Hydroxypropyl-β-Cyclodextrin
- (2012) Mark A. Crumling et al. PLoS One
- Long-Term Parenteral Administration of 2-Hydroxypropyl-β-Cyclodextrin Causes Bone Loss
- (2012) Ingrid Kantner et al. TOXICOLOGIC PATHOLOGY
- Quantitative role of LAL, NPC2, and NPC1 in lysosomal cholesterol processing defined by genetic and pharmacological manipulations
- (2011) Charina M. Ramirez et al. JOURNAL OF LIPID RESEARCH
- Unesterified Cholesterol Accumulation in Late Endosomes/Lysosomes Causes Neurodegeneration and Is Prevented by Driving Cholesterol Export from This Compartment
- (2011) A. Aqul et al. JOURNAL OF NEUROSCIENCE
- Corneal Alterations during Combined Therapy with Cyclodextrin/Allopregnanolone and Miglustat in a Knock-Out Mouse Model of NPC1 Disease
- (2011) Marine Hovakimyan et al. PLoS One
- Molecular Mechanism of Cyclodextrin Mediated Cholesterol Extraction
- (2011) Cesar A. López et al. PLoS Computational Biology
- Protection afforded by a herbal medicine, Sho-seiryu-to (TJ-19), against oleic acid-induced acute lung injury in guinea-pigs
- (2010) Chang-qing Yang et al. JOURNAL OF PHARMACY AND PHARMACOLOGY
- Pharmaceutical applications of cyclodextrins: basic science and product development
- (2010) Thorsteinn Loftsson et al. JOURNAL OF PHARMACY AND PHARMACOLOGY
- Niemann-Pick disease type C
- (2010) Marie T Vanier Orphanet Journal of Rare Diseases
- 2-Hydroxypropyl-β-Cyclodextrin Raises Hearing Threshold in Normal Cats and in Cats With Niemann-Pick Type C Disease
- (2010) Sarah Ward et al. PEDIATRIC RESEARCH
- Weekly Cyclodextrin Administration Normalizes Cholesterol Metabolism in Nearly Every Organ of the Niemann-Pick Type C1 Mouse and Markedly Prolongs Life
- (2010) Charina M Ramirez et al. PEDIATRIC RESEARCH
- Cyclodextrin Induces Calcium-Dependent Lysosomal Exocytosis
- (2010) Fannie W. Chen et al. PLoS One
- Endocytosis of beta-cyclodextrins is responsible for cholesterol reduction in Niemann-Pick type C mutant cells
- (2010) A. I. Rosenbaum et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Effects of Bolus Injection of Soybean-Based Fat Emulsion and Fatty Acids on Pulmonary Gas Exchange Function
- (2009) Yoichi Ishitsuka et al. BIOLOGICAL & PHARMACEUTICAL BULLETIN
- Structure of N-Terminal Domain of NPC1 Reveals Distinct Subdomains for Binding and Transfer of Cholesterol
- (2009) Hyock Joo Kwon et al. CELL
- A Selective Thromboxane A2 (TXA2) Synthase Inhibitor, Ozagrel, Attenuates Lung Injury and Decreases Monocyte Chemoattractant Protein-1 and Interleukin-8 mRNA Expression in Oleic Acid–Induced Lung Injury in Guinea Pigs
- (2009) Yoichi Ishitsuka et al. JOURNAL OF PHARMACOLOGICAL SCIENCES
- Chronic Cyclodextrin Treatment of Murine Niemann-Pick C Disease Ameliorates Neuronal Cholesterol and Glycosphingolipid Storage and Disease Progression
- (2009) Cristin D. Davidson et al. PLoS One
- Cyclodextrin overcomes deficient lysosome-to-endoplasmic reticulum transport of cholesterol in Niemann-Pick type C cells
- (2009) L. Abi-Mosleh et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Reversal of defective lysosomal transport in NPC disease ameliorates liver dysfunction and neurodegeneration in the npc1-/- mouse
- (2009) B. Liu et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- The pathogenesis of Niemann–Pick type C disease: a role for autophagy?
- (2008) Chris D. Pacheco et al. EXPERT REVIEWS IN MOLECULAR MEDICINE
- Study of the cholesterol extraction capacity of β-cyclodextrin and its derivatives, relationships with their effects on endothelial cell viability and on membrane models
- (2008) Delphine Castagne et al. JOURNAL OF INCLUSION PHENOMENA AND MACROCYCLIC CHEMISTRY
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