Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological disease progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1–2 trial

标题
Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological disease progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1–2 trial
作者
关键词
-
出版物
LANCET
Volume 390, Issue 10104, Pages 1758-1768
出版商
Elsevier BV
发表日期
2017-08-11
DOI
10.1016/s0140-6736(17)31465-4

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