Inclusion Solves Insolubility —Translational Research Cycle from Bedside to Bench and Bench to Bedside for Drug Development Targeting Niemann-Pick Disease Type C—
出版年份 2022 全文链接
标题
Inclusion Solves Insolubility —Translational Research Cycle from Bedside to Bench and Bench to Bedside for Drug Development Targeting Niemann-Pick Disease Type C—
作者
关键词
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出版物
YAKUGAKU ZASSHI-JOURNAL OF THE PHARMACEUTICAL SOCIETY OF JAPAN
Volume 142, Issue 4, Pages 389-400
出版商
Pharmaceutical Society of Japan
发表日期
2022-04-01
DOI
10.1248/yakushi.21-00215
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注意:仅列出部分参考文献,下载原文获取全部文献信息。- Intracerebroventricular Treatment with 2-Hydroxypropyl-β-Cyclodextrin Decreased Cerebellar and Hepatic Glycoprotein Nonmetastatic Melanoma Protein B (GPNMB) Expression in Niemann–Pick Disease Type C Model Mice
- (2021) Madoka Fukaura et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Differential mode of cholesterol inclusion with 2‐hydroxypropyl‐cyclodextrins increases safety margin in treatment of Niemann‐Pick disease type C
- (2021) Yusei Yamada et al. BRITISH JOURNAL OF PHARMACOLOGY
- Improved systemic AAV gene therapy with a neurotrophic capsid in Niemann–Pick disease type C1 mice
- (2021) Cristin D Davidson et al. Life Science Alliance
- Differential Effects of 2-Hydroxypropyl-Cyclodextrins on Lipid Accumulation in Npc1-Null Cells
- (2020) Sanzana Hoque et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- In Vitro and In Vivo Evaluation of 6-O-α-Maltosyl-β-Cyclodextrin as a Potential Therapeutic Agent Against Niemann-Pick Disease Type C
- (2019) Nushrat Yasmin et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- In vivo Efficacy and Safety Evaluation of Lactosyl-β-cyclodextrin as a Therapeutic Agent for Hepatomegaly in Niemann-Pick Type C Disease
- (2019) Yuki Maeda et al. Nanomaterials
- Role of 6- O -α-maltosyl-β-cyclodextrin in lysosomal cholesterol deprivation in Npc1- deficient Chinese hamster ovary cells
- (2018) Yasuyo Okada et al. CARBOHYDRATE RESEARCH
- Predicting the Binding Mode of 2-Hydroxypropyl-β-cyclodextrin to Cholesterol by Means of the MD Simulation and the 3D-RISM-KH Theory
- (2018) Yuji Hayashino et al. JOURNAL OF PHYSICAL CHEMISTRY B
- Impact of the Niemann–Pick c1 Gene Mutation on the Total Cellular Glycomics of CHO Cells
- (2017) Jun-ichi Furukawa et al. JOURNAL OF PROTEOME RESEARCH
- Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological disease progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1–2 trial
- (2017) Daniel S Ory et al. LANCET
- Cyclodextrins and Iatrogenic Hearing Loss: New Drugs with Significant Risk
- (2017) Mark A. Crumling et al. Frontiers in Cellular Neuroscience
- In vitro evaluation of 2-hydroxyalkylated β-cyclodextrins as potential therapeutic agents for Niemann-Pick Type C disease
- (2016) Yuki Kondo et al. MOLECULAR GENETICS AND METABOLISM
- Efficacy of 2-Hydroxypropyl-β-cyclodextrin in Niemann–Pick Disease Type C Model Mice and Its Pharmacokinetic Analysis in a Patient with the Disease
- (2015) Yuta Tanaka et al. BIOLOGICAL & PHARMACEUTICAL BULLETIN
- β-Cyclodextrin-threaded Biocleavable Polyrotaxanes Ameliorate Impaired Autophagic Flux in Niemann-Pick Type C Disease
- (2015) Atsushi Tamura et al. JOURNAL OF BIOLOGICAL CHEMISTRY
- HPGCD Outperforms HPBCD as a Potential Treatment for Niemann-Pick Disease Type C During Disease Modeling with iPS Cells
- (2015) Minami Soga et al. STEM CELLS
- 2-Hydroxypropyl-β-Cyclodextrin Acts as a Novel Anticancer Agent
- (2015) Masako Yokoo et al. PLoS One
- Population pharmacokinetics of doxapram in low-birth-weight Japanese infants with apnea
- (2014) Yuki Ogawa et al. EUROPEAN JOURNAL OF PEDIATRICS
- Reply: Lung toxicity of hydroxyl-β-cyclodextrin infusion
- (2013) Muneaki Matsuo et al. MOLECULAR GENETICS AND METABOLISM
- Lung toxicity of hydroxypropyl-β-cyclodextrin infusion
- (2013) Yin-Hsiu Chien et al. MOLECULAR GENETICS AND METABOLISM
- Comparative effects of respiratory stimulants on hypoxic neuronal cell injury in SH-SY5Y cells and in hippocampal slice cultures from rat pups
- (2013) Kaori Tanaka et al. PEDIATRICS INTERNATIONAL
- Aminophylline, administered at usual doses for rodents in pharmacological studies, induces hippocampal neuronal cell injury under low tidal volume hypoxic conditions in guinea-pigs
- (2012) Tomoko Somekawa-Kondo et al. JOURNAL OF PHARMACY AND PHARMACOLOGY
- Effects of cyclodextrin in two patients with Niemann–Pick Type C disease
- (2012) Muneaki Matsuo et al. MOLECULAR GENETICS AND METABOLISM
- Long-Term Parenteral Administration of 2-Hydroxypropyl-β-Cyclodextrin Causes Bone Loss
- (2012) Ingrid Kantner et al. TOXICOLOGIC PATHOLOGY
- Evaluation of the vancomycin dosage regimen based on serum creatinine used in the neonatal intensive care unit
- (2011) Mitsuru Irikura et al. PEDIATRICS INTERNATIONAL
- Niemann-Pick disease type C
- (2010) Marie T Vanier Orphanet Journal of Rare Diseases
- Structure of N-Terminal Domain of NPC1 Reveals Distinct Subdomains for Binding and Transfer of Cholesterol
- (2009) Hyock Joo Kwon et al. CELL
- Reversal of defective lysosomal transport in NPC disease ameliorates liver dysfunction and neurodegeneration in the npc1-/- mouse
- (2009) B. Liu et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Methyl-Beta-Cyclodextrin Improves Fertilizing Ability of C57BL/6 Mouse Sperm after Freezing and Thawing by Facilitating Cholesterol Efflux from the Cells1
- (2007) Toru Takeo et al. BIOLOGY OF REPRODUCTION
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