标题
Capsid-specific removal of circulating antibodies to adeno-associated virus vectors
作者
关键词
-
出版物
Scientific Reports
Volume 10, Issue 1, Pages -
出版商
Springer Science and Business Media LLC
发表日期
2020-01-21
DOI
10.1038/s41598-020-57893-z
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Adeno-associated virus vector as a platform for gene therapy delivery
- (2019) Dan Wang et al. NATURE REVIEWS DRUG DISCOVERY
- Therapeutic plasma apheresis: Expertise and indications
- (2019) Djuna Z. de Back et al. TRANSFUSION AND APHERESIS SCIENCE
- Onasemnogene Abeparvovec: First Global Approval
- (2019) Sheridan M. Hoy DRUGS
- AAV8 virions hijack serum proteins to increase hepatocyte binding for transduction enhancement
- (2018) Xiaolei Pei et al. VIROLOGY
- Influence of Pre-existing Anti-capsid Neutralizing and Binding Antibodies on AAV Vector Transduction
- (2018) Zachary Fitzpatrick et al. Molecular Therapy-Methods & Clinical Development
- Emerging Issues in AAV-Mediated In Vivo Gene Therapy
- (2018) Pasqualina Colella et al. Molecular Therapy-Methods & Clinical Development
- Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration
- (2018) Amine Meliani et al. Nature Communications
- Unraveling the Complex Story of Immune Responses to AAV Vectors Trial After Trial
- (2017) Céline Vandamme et al. HUMAN GENE THERAPY
- Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
- (2017) Jerry R. Mendell et al. NEW ENGLAND JOURNAL OF MEDICINE
- Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant
- (2017) Lindsey A. George et al. NEW ENGLAND JOURNAL OF MEDICINE
- AAV5–Factor VIII Gene Transfer in Severe Hemophilia A
- (2017) Savita Rangarajan et al. NEW ENGLAND JOURNAL OF MEDICINE
- Therapeutic Apheresis in Immunologic Renal and Neurological Diseases
- (2017) Rolf Bambauer et al. THERAPEUTIC APHERESIS AND DIALYSIS
- Direct interaction of human serum proteins with AAV virions to enhance AAV transduction: immediate impact on clinical applications
- (2016) M Wang et al. GENE THERAPY
- Determination of Anti-Adeno-Associated Virus Vector Neutralizing Antibody Titer with anIn VitroReporter System
- (2015) Amine Meliani et al. Human Gene Therapy Methods
- Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning
- (2015) Manuela Corti et al. Human Gene Therapy Clinical Development
- AAV capsid CD8+ T-cell epitopes are highly conserved across AAV serotypes
- (2015) Daniel J Hui et al. Molecular Therapy-Methods & Clinical Development
- Life-Long Correction of Hyperbilirubinemia with a Neonatal Liver-Specific AAV-Mediated Gene Transfer in a Lethal Mouse Model of Crigler–Najjar Syndrome
- (2014) Giulia Bortolussi et al. HUMAN GENE THERAPY
- Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B
- (2014) Amit C. Nathwani et al. NEW ENGLAND JOURNAL OF MEDICINE
- Plasmapheresis Eliminates the Negative Impact of AAV Antibodies on Microdystrophin Gene Expression Following Vascular Delivery
- (2013) LG Chicoine et al. MOLECULAR THERAPY
- Overcoming Preexisting Humoral Immunity to AAV Using Capsid Decoys
- (2013) F. Mingozzi et al. Science Translational Medicine
- Prevalence and pharmacological modulation of humoral immunity to AAV vectors in gene transfer to synovial tissue
- (2012) F Mingozzi et al. GENE THERAPY
- Humoral and Cellular Capsid-Specific Immune Responses to Adeno-Associated Virus Type 1 in Randomized Healthy Donors
- (2012) P. Veron et al. JOURNAL OF IMMUNOLOGY
- Endgame: Glybera Finally Recommended for Approval as the First Gene Therapy Drug in the European Union
- (2012) Seppo Ylä-Herttuala MOLECULAR THERAPY
- Complications of Apheresis
- (2012) Andre Kaplan SEMINARS IN DIALYSIS
- Adeno-Associated Virus Antibody Profiles in Newborns, Children, and Adolescents
- (2011) Roberto Calcedo et al. Clinical and Vaccine Immunology
- Neutralizing antibodies against adeno-associated virus examined prospectively in pediatric patients with hemophilia
- (2011) C Li et al. GENE THERAPY
- A 10 Patient Case Report on the Impact of Plasmapheresis Upon Neutralizing Factors Against Adeno-associated Virus (AAV) Types 1, 2, 6, and 8
- (2011) Virginie Monteilhet et al. MOLECULAR THERAPY
- Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges
- (2011) Federico Mingozzi et al. NATURE REVIEWS GENETICS
- Prevalence of Serum IgG and Neutralizing Factors Against Adeno-Associated Virus (AAV) Types 1, 2, 5, 6, 8, and 9 in the Healthy Population: Implications for Gene Therapy Using AAV Vectors
- (2010) Sylvie Boutin et al. HUMAN GENE THERAPY
- Preexisting Immunity and Low Expression in Primates Highlight Translational Challenges for Liver-directed AAV8-mediated Gene Therapy
- (2010) Gregory D Hurlbut et al. MOLECULAR THERAPY
- High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency
- (2009) E Ayuso et al. GENE THERAPY
- Producing Recombinant Adeno-Associated Virus in Foster Cells: Overcoming Production Limitations Using a Baculovirus–Insect Cell Expression Strategy
- (2009) Tamas Virag et al. HUMAN GENE THERAPY
- Enhanced Exon-skipping Induced by U7 snRNA Carrying a Splicing Silencer Sequence: Promising Tool for DMD Therapy
- (2009) Aurélie Goyenvalle et al. MOLECULAR THERAPY
- The Pleiotropic Effects of Natural AAV Infections on Liver-directed Gene Transfer in Macaques
- (2009) Lili Wang et al. MOLECULAR THERAPY
- Antigen-specific Apheresis of Pathogenic Autoantibodies from Myasthenia Gravis Sera
- (2008) Socrates J. Tzartos et al. Annals of the New York Academy of Sciences
- Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis
- (2008) Albert M. Maguire et al. NEW ENGLAND JOURNAL OF MEDICINE
- Manipulation of the mechanical properties of a virus by protein engineering
- (2008) C. Carrasco et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
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