A multicenter open-label treatment protocol (HGT-GCB-058) of velaglucerase alfa enzyme replacement therapy in patients with Gaucher disease type 1: safety and tolerability

Enzyme replacement therapy with velaglucerase alfa in Gaucher disease: Results from a randomized, double-blind, multinational, Phase 3 study

(2012) Derlis E. Gonzalez et al.   AMERICAN JOURNAL OF HEMATOLOGY

Safety and efficacy of velaglucerase alfa in Gaucher disease type 1 patients previously treated with imiglucerase

(2012) Ari Zimran et al.   AMERICAN JOURNAL OF HEMATOLOGY

Velaglucerase alfa enzyme replacement therapy compared with imiglucerase in patients with Gaucher disease

(2012) Hadhami Ben Turkia et al.   AMERICAN JOURNAL OF HEMATOLOGY

Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease

(2011) A. Zimran et al.   BLOOD

Booster-effect with velaglucerase alfa in patients with Gaucher disease switched from long-term imiglucerase therapy: Early Access Program results from Jerusalem

(2011) Deborah Elstein et al.   BLOOD CELLS MOLECULES AND DISEASES

Development of a panel of highly sensitive, equivalent assays for detection of antibody responses to velaglucerase alfa or imiglucerase enzyme replacement therapy in patients with Gaucher disease

(2011) Márcia Séllos-Moura et al.   JOURNAL OF IMMUNOLOGICAL METHODS

Recombinant Glucocerebrosidase (Imiglucerase) as a Therapy for Gaucher Disease

(2010) Gregory M. Pastores   BIODRUGS

Phase 1/2 and extension study of velaglucerase alfa replacement therapy in adults with type 1 Gaucher disease: 48-month experience

(2010) A. Zimran et al.   BLOOD

A randomized trial comparing the efficacy and safety of imiglucerase (Cerezyme) infusions every 4 weeks versus every 2 weeks in the maintenance therapy of adult patients with Gaucher disease type 1

(2009) P.S. Kishnani et al.   MOLECULAR GENETICS AND METABOLISM

Gaucher disease: mutation and polymorphism spectrum in the glucocerebrosidase gene (GBA)

(2008) Kathleen S. Hruska et al.   HUMAN MUTATION