In utero administration of Ad5 and AAV pseudotypes to the fetal brain leads to efficient, widespread and long-term gene expression

TerminalN-Linked Galactose Is the Primary Receptor for Adeno-associated Virus 9

(2011) Shen Shen et al.   JOURNAL OF BIOLOGICAL CHEMISTRY

Efficient gene transfer into neurons in monkey brain by adeno-associated virus 8

(2010) Yoshito Masamizu et al.   NEUROREPORT

Intracranial gene delivery of LV-NAGLU vector corrects neuropathology in murine MPS IIIB

(2009) Carmela Di Domenico et al.   AMERICAN JOURNAL OF MEDICAL GENETICS PART A

Efficient gene delivery to the adult and fetal CNS using pseudotyped non-integrating lentiviral vectors

(2009) A A Rahim et al.   GENE THERAPY

Long-term AAV vector gene and protein expression in mouse brain from a small pan-cellular promoter is similar to neural cell promoters

(2009) T Husain et al.   GENE THERAPY

Efficient intracerebral delivery of AAV5 vector encoding human ARSA in non-human primate

(2009) M.-A. Colle et al.   HUMAN MOLECULAR GENETICS

Anatomical Characterization of Human Fetal Brain Development with Diffusion Tensor Magnetic Resonance Imaging

(2009) H. Huang et al.   JOURNAL OF NEUROSCIENCE

Efficient Gene Delivery and Selective Transduction of Glial Cells in the Mammalian Brain by AAV Serotypes Isolated From Nonhuman Primates

(2009) Patricia A Lawlor et al.   MOLECULAR THERAPY

Comparative Transduction Efficiency of AAV Vector Serotypes 1–6 in the Substantia Nigra and Striatum of the Primate Brain

(2009) Eleni A Markakis et al.   MOLECULAR THERAPY

Understanding microRNAs in neurodegeneration

(2009) Stephen M. Eacker et al.   NATURE REVIEWS NEUROSCIENCE

MicroRNAs Potentiate Neural Development

(2009) Sarah K. Fineberg et al.   NEURON

MicroRNAs couple cell fate and developmental timing in retina

(2009) Sarah Decembrini et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

Stem cell and genetic therapies for the fetus

(2009) Jessica L. Roybal et al.   Seminars in Fetal & Neonatal Medicine

Novel mutation and the first prenatal screening of cathepsin D deficiency (CLN10)

(2008) Karen Fritchie et al.   ACTA NEUROPATHOLOGICA

Epigenetic regulation of cytomegalovirus major immediate-early promoter activity in transgenic mice

(2008) Abhishek Kumar Mehta et al.   GENE

Primary neurons become less susceptible to coxsackievirus B5 following maturation: The correlation with the decreased level of CAR expression on cell surface

(2008) Jeonghyun Ahn et al.   JOURNAL OF MEDICAL VIROLOGY

Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes

(2008) Kevin D Foust et al.   NATURE BIOTECHNOLOGY

Gaucher disease

(2007) Pascal Guggenbuhl et al.   JOINT BONE SPINE