Revised recommendations for the management of Gaucher disease in children
Published 2012 View Full Article
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Title
Revised recommendations for the management of Gaucher disease in children
Authors
Keywords
Gaucher disease type 1, Gaucher disease type 2, Gaucher disease type 3, Glucocerebrosidase, Glucocerebroside, Enzyme replacement therapy, Genetic counseling, Monitoring, Disease management, Treatment recommendations
Journal
EUROPEAN JOURNAL OF PEDIATRICS
Volume 172, Issue 4, Pages 447-458
Publisher
Springer Nature
Online
2012-07-17
DOI
10.1007/s00431-012-1771-z
References
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