Evidence-based focused review of the status of hematopoietic stem cell transplantation as treatment of sickle cell disease and thalassemia

A Systematic Review of Barriers and Interventions to Improve Appropriate Use of Therapies for Sickle Cell Disease

(2016) Carlton Haywood et al.   JOURNAL OF THE NATIONAL MEDICAL ASSOCIATION

Growth and endocrine function in thalassemia major in childhood and adolescence

(2014) M. Delvecchio et al.   JOURNAL OF ENDOCRINOLOGICAL INVESTIGATION

Pretransplant Immunosuppression followed by Reduced-Toxicity Conditioning and Stem Cell Transplantation in High-Risk Thalassemia: A Safe Approach to Disease Control

(2013) Usanarat Anurathapan et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Long-Term Outcome and Evaluation of Organ Function in Pediatric Patients Undergoing Haploidentical and Matched Related Hematopoietic Cell Transplantation for Sickle Cell Disease

(2013) Mari H. Dallas et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Long-term health-related quality of life evaluated more than 20 years after hematopoietic stem cell transplantation for thalassemia

(2013) G. La Nasa et al.   BLOOD

Outcome of patients with hemoglobinopathies given either cord blood or bone marrow transplantation from an HLA-identical sibling

(2013) F. Locatelli et al.   BLOOD

Cost utility analysis of reduced intensity hematopoietic stem cell transplantation in adolescence and young adult with severe thalassemia compared to hypertransfusion and iron chelation program

(2013) Rosarin Sruamsiri et al.   BMC HEALTH SERVICES RESEARCH

Risk adopted allogeneic hematopoietic stem cell transplantation using a reduced intensity regimen for children with thalassemia major

(2013) Ayad Ahmed Hussein et al.   PEDIATRIC BLOOD & CANCER

Improved Clinical Outcomes of High Risk β Thalassemia Major Patients Undergoing a HLA Matched Related Allogeneic Stem Cell Transplant with a Treosulfan Based Conditioning Regimen and Peripheral Blood Stem Cell Grafts

(2013) Vikram Mathews et al.   PLoS One

Stem Cell Transplant for Children with Sickle Cell Anemia: Parent and Patient Interest

(2012) Michael Roth et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Unrelated Donor Cord Blood Transplantation for Children with Severe Sickle Cell Disease: Results of One Cohort from the Phase II Study from the Blood and Marrow Transplant Clinical Trials Network (BMT CTN)

(2012) Naynesh R. Kamani et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Treosulfan-Thiotepa-Fludarabine–Based Conditioning Regimen for Allogeneic Transplantation in Patients with Thalassemia Major: A Single-Center Experience from North India

(2012) Dharma Choudhary et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

French Multicenter 22-Year Experience in Stem Cell Transplantation for Beta-Thalassemia Major: Lessons and Future Directions

(2012) Claire Galambrun et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

A novel conditioning regimen improves outcomes in  -thalassemia major patients using unrelated donor peripheral blood stem cell transplantation

(2012) C. Li et al.   BLOOD

Allogeneic hematopoietic stem cell transplantation in thalassemia major: results of a reduced-toxicity conditioning regimen based on the use of treosulfan

(2012) M. E. Bernardo et al.   BLOOD

HLA-haploidentical bone marrow transplantation with posttransplant cyclophosphamide expands the donor pool for patients with sickle cell disease

(2012) J. Bolanos-Meade et al.   BLOOD

HLA-matched family hematopoetic stem cell transplantation in children with beta thalassemia major: The experience of the Turkish Pediatric Bone Marrow Transplantation Group

(2012) M. Akif Yesilipek et al.   PEDIATRIC TRANSPLANTATION

Umbilical Cord Blood Transplantation for Children with Thalassemia and Sickle Cell Disease

(2011) Annalisa Ruggeri et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Unrelated cord blood transplantation for thalassaemia: a single-institution experience of 35 patients

(2011) T-H Jaing et al.   BONE MARROW TRANSPLANTATION

Higher CD3+ and CD34+ cell doses in the graft increase the incidence of acute GVHD in children receiving BMT for thalassemia

(2011) J Gaziev et al.   BONE MARROW TRANSPLANTATION

Allogeneic cellular gene therapy in hemoglobinopathies—evaluation of hematopoietic SCT in sickle cell anemia

(2011) G Lucarelli et al.   BONE MARROW TRANSPLANTATION

Hydroxycarbamide in very young children with sickle-cell anaemia: a multicentre, randomised, controlled trial (BABY HUG)

(2011) Winfred C Wang et al.   LANCET

Bone marrow transplant options and preferences in a sickle cell anemia cohort on chronic transfusions

(2011) Eileen N. Hansbury et al.   PEDIATRIC BLOOD & CANCER

Sickle Cell Disease–Related Pediatric Medical Expenditures in the U.S.

(2010) Djesika D. Amendah et al.   AMERICAN JOURNAL OF PREVENTIVE MEDICINE

Prospective Assessment of Health-Related Quality of Life in Pediatric Patients with Beta-Thalassemia following Hematopoietic Stem Cell Transplantation

(2010) Giovanni Caocci et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Silent cerebral infarcts occur despite regular blood transfusion therapy after first strokes in children with sickle cell disease

(2010) M. L. Hulbert et al.   BLOOD

HLA-matched sibling bone marrow transplantation for  -thalassemia major

(2010) M. Sabloff et al.   BLOOD

In mixed hematopoietic chimerism, the donor red cells win

(2010) M. M. Hsieh et al.   HAEMATOLOGICA

Unpredictability of Intravenous Busulfan Pharmacokinetics in Children Undergoing Hematopoietic Stem Cell Transplantation for Advanced Beta Thalassemia: Limited Toxicity with a Dose-Adjustment Policy

(2009) Robert Chiesa et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Pulmonary, Gonadal, and Central Nervous System Status after Bone Marrow Transplantation for Sickle Cell Disease

(2009) Mark C. Walters et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

The effect of prolonged administration of hydroxyurea on morbidity and mortality in adult patients with sickle cell syndromes: results of a 17-year, single-center trial (LaSHS)

(2009) E. Voskaridou et al.   BLOOD

Silent infarcts in young children with sickle cell disease

(2009) Janet L. Kwiatkowski et al.   BRITISH JOURNAL OF HAEMATOLOGY

Decision Analysis of Treatment Strategies in Children With Severe Sickle Cell Disease

(2009) Sarah H. OʼBrien et al.   JOURNAL OF PEDIATRIC HEMATOLOGY ONCOLOGY

Allogeneic Hematopoietic Stem-Cell Transplantation for Sickle Cell Disease

(2009) Matthew M. Hsieh et al.   NEW ENGLAND JOURNAL OF MEDICINE

Stable Long-Term Donor Engraftment following Reduced-Intensity Hematopoietic Cell Transplantation for Sickle Cell Disease

(2008) Lakshmanan Krishnamurti et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION