Factor IX ectopically expressed in platelets can be stored in  -granules and corrects the phenotype of hemophilia B mice

Adipose tissue is an extramedullary reservoir for functional hematopoietic stem and progenitor cells

(2009) J. Han et al.   BLOOD

Platelet α-granules: Basic biology and clinical correlates

(2009) Price Blair et al.   BLOOD REVIEWS

Syngeneic transplantation of hematopoietic stem cells that are genetically modified to express factor VIII in platelets restores hemostasis to hemophilia A mice with preexisting FVIII immunity

(2008) Q. Shi et al.   BLOOD

Long-term correction of inhibitor-prone hemophilia B dogs treated with liver-directed AAV2-mediated factor IX gene therapy

(2008) G. P. Niemeyer et al.   BLOOD

AAV-mediated gene transfer for the treatment of hemophilia B: problems and prospects

(2008) N C Hasbrouck et al.   GENE THERAPY

Phenotypic Correction of Hemophilia A by Ectopic Expression of Activated Factor VII in Platelets

(2008) Tsukasa Ohmori et al.   MOLECULAR THERAPY

Erythroid-specific Human Factor IX Delivery From In Vivo Selected Hematopoietic Stem Cells Following Nonmyeloablative Conditioning in Hemophilia B Mice

(2008) Alex H Chang et al.   MOLECULAR THERAPY