Competing for the treasure in exceptions

Development of a panel of highly sensitive, equivalent assays for detection of antibody responses to velaglucerase alfa or imiglucerase enzyme replacement therapy in patients with Gaucher disease

(2011) Márcia Séllos-Moura et al.   JOURNAL OF IMMUNOLOGICAL METHODS

Osseous Manifestations of Adult Gaucher Disease in the Era of Enzyme Replacement Therapy

(2011) Patrick B. Deegan et al.   MEDICINE

European regulation on orphan medicinal products: 10 years of experience and future perspectives

(2011)   NATURE REVIEWS DRUG DISCOVERY

Velaglucerase alfa

(2010) Johannes M. F. G. Aerts et al.   NATURE REVIEWS DRUG DISCOVERY

Force Majeure: Therapeutic measures in response to restricted supply of imiglucerase (Cerezyme) for patients with Gaucher disease

(2009) Carla E.M. Hollak et al.   BLOOD CELLS MOLECULES AND DISEASES

Characterization of gene-activated human acid- -glucosidase: Crystal structure, glycan composition, and internalization into macrophages

(2009) B. Brumshtein et al.   GLYCOBIOLOGY