Therapeutic Genome Editing With CRISPR/Cas9 in a Humanized Mouse Model Ameliorates α1-antitrypsin Deficiency Phenotype

Title
Therapeutic Genome Editing With CRISPR/Cas9 in a Humanized Mouse Model Ameliorates α1-antitrypsin Deficiency Phenotype
Authors
Keywords
-
Journal
EBioMedicine
Volume 29, Issue -, Pages 104-111
Publisher
Elsevier BV
Online
2018-02-20
DOI
10.1016/j.ebiom.2018.02.015

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