A checklist for clinical trials in rare disease: obstacles and anticipatory actions—lessons learned from the FOR-DMD trial
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Title
A checklist for clinical trials in rare disease: obstacles and anticipatory actions—lessons learned from the FOR-DMD trial
Authors
Keywords
Clinical trial, Academic-led clinical trial, Clinical trial regulations, Duchenne muscular dystrophy, Rare disease
Journal
Trials
Volume 19, Issue 1, Pages -
Publisher
Springer Nature
Online
2018-05-24
DOI
10.1186/s13063-018-2645-0
References
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