Creation of Dystrophin Expressing Chimeric Cells of Myoblast Origin as a Novel Stem Cell Based Therapy for Duchenne Muscular Dystrophy

Can Human Embryonic Stem Cell-Derived Stromal Cells Serve a Starting Material for Myoblasts?

(2017) Yu Ando et al.   Stem Cells International

Adaptive Immune Response Impairs the Efficacy of Autologous Transplantation of Engineered Stem Cells in Dystrophic Dogs

(2016) Clementina Sitzia et al.   MOLECULAR THERAPY

Confirmation of donor-derived dystrophin in a duchenne muscular dystrophy patient allotransplanted with normal myoblasts

(2016) Daniel Skuk et al.   MUSCLE & NERVE

Transplantation of Human Adipose Mesenchymal Stem Cells in Non-Immunosuppressed GRMD Dogs is a Safe Procedure

(2016) M. V. Pelatti et al.   Stem Cell Reviews and Reports

Prosurvival Factors Improve Functional Engraftment of Myogenically Converted Dermal Cells into Dystrophic Skeletal Muscle

(2016) Lindsey A. Muir et al.   STEM CELLS AND DEVELOPMENT

Autologous skeletal muscle derived cells expressing a novel functional dystrophin provide a potential therapy for Duchenne Muscular Dystrophy

(2016) Jinhong Meng et al.   Scientific Reports

Transplantation of Human Adipose Mesenchymal Stem Cells in Non-Immunosuppressed GRMD Dogs is a Safe Procedure

(2016) M. V. Pelatti et al.   Stem Cell Reviews and Reports

Adenoviral vectors encoding CRISPR/Cas9 multiplexes rescue dystrophin synthesis in unselected populations of DMD muscle cells

(2016) Ignazio Maggio et al.   Scientific Reports

Recent advances in the management of Duchenne muscular dystrophy

(2015) Eugen-Matthias Strehle et al.   ARCHIVES OF DISEASE IN CHILDHOOD

Immunomodulatory Effects of Different Cellular Therapies of Bone Marrow Origin on Chimerism Induction and Maintenance Across MHC Barriers in a Face Allotransplantation Model

(2015) Mikael Hivelin et al.   ARCHIVUM IMMUNOLOGIAE ET THERAPIAE EXPERIMENTALIS

Intra-arterial transplantation of HLA-matched donor mesoangioblasts in Duchenne muscular dystrophy

(2015) G. Cossu et al.   EMBO Molecular Medicine

Cell therapy in muscular dystrophies: many promises in mice and dogs, few facts in patients

(2015) Daniel Skuk et al.   EXPERT OPINION ON BIOLOGICAL THERAPY

Long-term engraftment of myogenic progenitors from adipose-derived stem cells and muscle regeneration in dystrophic mice

(2015) Yu Zhang et al.   HUMAN MOLECULAR GENETICS

Differentiation of pluripotent stem cells to muscle fiber to model Duchenne muscular dystrophy

(2015) Jérome Chal et al.   NATURE BIOTECHNOLOGY

In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy

(2015) C. E. Nelson et al.   SCIENCE

Isolation and Immortalization of Patient-derived Cell Lines from Muscle Biopsy for Disease Modeling

(2015) Jerome D. Robin et al.   Jove-Journal of Visualized Experiments

Duchenne muscular dystrophy: current cell therapies

(2015) Dorota Sienkiewicz et al.   Therapeutic Advances in Neurological Disorders

Inflammation Converts Human Mesoangioblasts Into Targets of Alloreactive Immune Responses: Implications for Allogeneic Cell Therapy of DMD

(2014) Maddalena Noviello et al.   MOLECULAR THERAPY

Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA

(2014) C. Long et al.   SCIENCE

Human Adipose Tissue Derived Pericytes Increase Life Span in Utrn tm1Ked Dmd mdx /J Mice

(2014) M. C. Valadares et al.   Stem Cell Reviews and Reports

Engraftment potential of dermal fibroblasts following in vivo myogenic conversion in immunocompetent dystrophic skeletal muscle

(2014) Lindsey A Muir et al.   Molecular Therapy-Methods & Clinical Development

Ongoing therapeutic trials and outcome measures for Duchenne muscular dystrophy

(2013) Alessandra Govoni et al.   CELLULAR AND MOLECULAR LIFE SCIENCES

Application of Cell-Based Therapies in Facial Transplantation

(2012) Maria Siemionow et al.   ANNALS OF PLASTIC SURGERY

Myoblasts Derived From Normal hESCs and Dystrophic hiPSCs Efficiently Fuse With Existing Muscle Fibers Following Transplantation

(2012) Sébastien Goudenege et al.   MOLECULAR THERAPY

Donor Satellite Cell Engraftment Is SignificantlyAugmented When the Host Niche Is Preserved and Endogenous Satellite Cells Are Incapacitated

(2012) Luisa Boldrin et al.   STEM CELLS

A Simplified Immune Suppression Scheme Leads to Persistent Micro-dystrophin Expression in Duchenne Muscular Dystrophy Dogs

(2011) Jin-Hong Shin et al.   HUMAN GENE THERAPY

Long-term Engraftment of Multipotent Mesenchymal Stromal Cells That Differentiate to Form Myogenic Cells in Dogs With Duchenne Muscular Dystrophy

(2011) Yuko Nitahara-Kasahara et al.   MOLECULAR THERAPY

Physiological Characterization of Muscle Strength With Variable Levels of Dystrophin Restoration in mdx Mice Following Local Antisense Therapy

(2010) Paul S Sharp et al.   MOLECULAR THERAPY

Past, present and future of myoblast transplantation in the treatment of Duchenne muscular dystrophy

(2010) Beniamino Palmieri et al.   PEDIATRIC TRANSPLANTATION

Long-Term Survival of Composite Hemiface/Mandible/Tongue Allografts Correlates With Multilineage Chimerism Development in the Lymphoid and Myeloid Compartments of Recipients

(2010) Yalcin Kulahci et al.   TRANSPLANTATION

Near-total human face transplantation for a severely disfigured patient in the USA

(2009) Maria Siemionow et al.   LANCET

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

(2009) Maria Kinali et al.   LANCET NEUROLOGY

Hematopoietic Stem Cell Engraftment and Seeding Permits Multi-Lymphoid Chimerism in Vascularized Bone Marrow Transplants

(2008) M. Siemionow et al.   AMERICAN JOURNAL OF TRANSPLANTATION