4.2 Editorial Material

Severe persistent injection site reactions after subcutaneous 2′-O-methyl phosphorothioate oligonucleotide therapy for Duchenne muscular dystrophy

Journal

NEUROMUSCULAR DISORDERS
Volume 28, Issue 2, Pages 176-177

Publisher

PERGAMON-ELSEVIER SCIENCE LTD
DOI: 10.1016/j.nmd.2017.11.015

Keywords

Antisense oligonucleotide; Exon skipping; Subcutaneous injections; Morphea-like skin lesion; Duchenne muscular dystrophy

Funding

  1. National Institute for Health Research [NF-SI-0515-10022] Funding Source: researchfish

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