Journal
NEUROMUSCULAR DISORDERS
Volume 28, Issue 2, Pages 176-177Publisher
PERGAMON-ELSEVIER SCIENCE LTD
DOI: 10.1016/j.nmd.2017.11.015
Keywords
Antisense oligonucleotide; Exon skipping; Subcutaneous injections; Morphea-like skin lesion; Duchenne muscular dystrophy
Categories
Funding
- National Institute for Health Research [NF-SI-0515-10022] Funding Source: researchfish