Agreement between the results of meta-analyses from case reports and from clinical studies regarding the efficacy of laronidase therapy in patients with mucopolysaccharidosis type I who initiated enzyme replacement therapy in adult age: An example of case reports meta-analyses as an useful tool for evidence-based medicine in rare diseases

Title

Agreement between the results of meta-analyses from case reports and from clinical studies regarding the efficacy of laronidase therapy in patients with mucopolysaccharidosis type I who initiated enzyme replacement therapy in adult age: An example of case reports meta-analyses as an useful tool for evidence-based medicine in rare diseases

Authors

Keywords

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Journal

MOLECULAR GENETICS AND METABOLISM

Volume 123, Issue 2, Pages 69-75

Publisher

Elsevier BV

Online

2018-01-06

DOI

10.1016/j.ymgme.2018.01.002