Repairing folding-defective α-sarcoglycan mutants by CFTR correctors, a potential therapy for limb-girdle muscular dystrophy 2D
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Title
Repairing folding-defective α-sarcoglycan mutants by CFTR correctors, a potential therapy for limb-girdle muscular dystrophy 2D
Authors
Keywords
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Journal
HUMAN MOLECULAR GENETICS
Volume 27, Issue 6, Pages 969-984
Publisher
Oxford University Press (OUP)
Online
2018-01-16
DOI
10.1093/hmg/ddy013
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