In Utero Transplantation of Placenta-Derived Mesenchymal Stromal Cells for Potential Fetal Treatment of Hemophilia A

Functional Correction of Large Factor VIII Gene Chromosomal Inversions in Hemophilia A Patient-Derived iPSCs Using CRISPR-Cas9

(2015) Chul-Yong Park et al.   Cell Stem Cell

Mesenchymal stem cell treatment for hemophilia: a review of current knowledge

(2015) E. M. Sokal et al.   JOURNAL OF THROMBOSIS AND HAEMOSTASIS

Placental Mesenchymal Stromal Cells Rescue Ambulation in Ovine Myelomeningocele

(2015) Aijun Wang et al.   Stem Cells Translational Medicine

Early gestation chorionic villi-derived stromal cells for fetal tissue engineering

(2015) Lee Lankford   World Journal of Stem Cells

Recombinant factor VIII products and inhibitor development in previously untreated boys with severe hemophilia A

(2014) T. Calvez et al.   BLOOD

Hemophilia A: an ideal disease to correct in utero

(2014) Christopher D. Porada et al.   Frontiers in Pharmacology

The Mesenchymal Stem Cells Derived from Transgenic Mice Carrying Human Coagulation Factor VIII Can Correct Phenotype in Hemophilia A Mice

(2013) Qing Wang et al.   Journal of Genetics and Genomics

Factor VIII Products and Inhibitor Development in Severe Hemophilia A

(2013) Samantha C. Gouw et al.   NEW ENGLAND JOURNAL OF MEDICINE

Production of Factor VIII by Human Liver Sinusoidal Endothelial Cells Transplanted in Immunodeficient uPA Mice

(2013) Marina E. Fomin et al.   PLoS One

In utero transplantation: Disparate ramifications

(2013) John S Pixley   World Journal of Stem Cells

Generation of an optimized lentiviral vector encoding a high-expression factor VIII transgene for gene therapy of hemophilia A

(2012) J M Johnston et al.   GENE THERAPY

Endothelial progenitor cell-based therapy for hemophilia A

(2012) Hideto Matsui   INTERNATIONAL JOURNAL OF HEMATOLOGY

Phenotypic correction of hemophilia A in sheep by postnatal intraperitoneal transplantation of FVIII-expressing MSC

(2011) Christopher D. Porada et al.   EXPERIMENTAL HEMATOLOGY

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

(2011) Amit C. Nathwani et al.   NEW ENGLAND JOURNAL OF MEDICINE

Targeting FVIII expression to endothelial cells regenerates a releasable pool of FVIII and restores hemostasis in a mouse model of hemophilia A

(2010) Q. Shi et al.   BLOOD

Sites of initial bleeding episodes, mode of delivery and age of diagnosis in babies with haemophilia diagnosed before the age of 2 years: a report from The Centers for Disease Control and Prevention’s (CDC) Universal Data Collection (UDC) project

(2009) R. KULKARNI et al.   HAEMOPHILIA

Phenotypic correction of murine hemophilia A using an iPS cell-based therapy

(2009) Dan Xu et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

Stem cell and genetic therapies for the fetus

(2009) Jessica L. Roybal et al.   Seminars in Fetal & Neonatal Medicine

Engraftment potential of human placenta-derived mesenchymal stem cells after in utero transplantation in rats

(2008) Chie-Pein Chen et al.   HUMAN REPRODUCTION

Fetal stem-cell transplantation

(2007) Eleonor Tiblad et al.   BEST PRACTICE & RESEARCH CLINICAL OBSTETRICS & GYNAECOLOGY