In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model

Title
In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model
Authors
Keywords
intrauterine gene transfer, adeno-associated viral vector, vector integration, non-human primate, immune tolerance, long-term expression, non-responder
Journal
MOLECULAR THERAPY
Volume 25, Issue 8, Pages 1843-1853
Publisher
Elsevier BV
Online
2017-04-25
DOI
10.1016/j.ymthe.2017.04.003

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