Mortality after hematopoietic stem cell transplantation for severe mucopolysaccharidosis type I: the 30-year University of Minnesota experience

Enzyme replacement therapy prior to haematopoietic stem cell transplantation in Mucopolysaccharidosis Type I: 10year combined experience of 2 centres

(2016) Arunabha Ghosh et al.   MOLECULAR GENETICS AND METABOLISM

Long-term outcome of Hurler syndrome patients after hematopoietic cell transplantation: an international multicenter study

(2015) M. Aldenhoven et al.   BLOOD

Outcomes of transplantation using various hematopoietic cell sources in children with Hurler syndrome after myeloablative conditioning

(2013) J. J. Boelens et al.   BLOOD

Non-TBI Hematopoietic Stem Cell Transplantation in Pediatric AML Patients

(2013) Amir A. Hamidieh et al.   JOURNAL OF PEDIATRIC HEMATOLOGY ONCOLOGY

Outcomes of haematopoietic stem cell transplantation for inherited metabolic disorders: A report from the Australian and New Zealand Children's Haematology Oncology Group and the Australasian Bone Marrow Transplant Recipient Registry

(2013) R. Mitchell et al.   PEDIATRIC TRANSPLANTATION

Risk Factor Analysis of Outcomes after Unrelated Cord Blood Transplantation in Patients with Hurler Syndrome

(2009) Jaap Jan Boelens et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Pre-transplant risk factors affecting outcome in Hurler syndrome

(2009) P J Orchard et al.   BONE MARROW TRANSPLANTATION

Advances in the Selection of HLA-Compatible Donors: Refinements in HLA Typing and Matching over the First 20 Years of the National Marrow Donor Program Registry

(2008) Stephen Spellman et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

The prevalence of and survival in Mucopolysaccharidosis I: Hurler, Hurler-Scheie and Scheie syndromes in the UK

(2008) David Moore et al.   Orphanet Journal of Rare Diseases