A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
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Title
A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
Authors
Keywords
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Journal
NATURE BIOTECHNOLOGY
Volume 34, Issue 3, Pages 334-338
Publisher
Springer Nature
Online
2016-02-01
DOI
10.1038/nbt.3469
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