Optimization of Morpholino Antisense Oligonucleotides Targeting the Intronic Repressor Element1 in Spinal Muscular Atrophy

Title
Optimization of Morpholino Antisense Oligonucleotides Targeting the Intronic Repressor Element1 in Spinal Muscular Atrophy
Authors
Keywords
-
Journal
MOLECULAR THERAPY
Volume 24, Issue 9, Pages 1592-1601
Publisher
Elsevier BV
Online
2016-07-12
DOI
10.1038/mt.2016.145

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