Enzyme replacement for GM1-gangliosidosis: Uptake, lysosomal activation, and cellular disease correction using a novel β-galactosidase:RTB lectin fusion

Title
Enzyme replacement for GM1-gangliosidosis: Uptake, lysosomal activation, and cellular disease correction using a novel β-galactosidase:RTB lectin fusion
Authors
Keywords
GM1-gangliosidosis, Lysosomal β-galactosidase, Lectin-mediated delivery, Plant-based bioproduction, RTB lectin
Journal
MOLECULAR GENETICS AND METABOLISM
Volume 117, Issue 2, Pages 199-209
Publisher
Elsevier BV
Online
2015-12-13
DOI
10.1016/j.ymgme.2015.12.002

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