Artificial microRNA suppresses C9ORF72 variants and decreases toxic dipeptide repeat proteins in vivo
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Title
Artificial microRNA suppresses C9ORF72 variants and decreases toxic dipeptide repeat proteins in vivo
Authors
Keywords
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Journal
GENE THERAPY
Volume -, Issue -, Pages -
Publisher
Springer Science and Business Media LLC
Online
2023-09-26
DOI
10.1038/s41434-023-00418-w
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