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Title
Gene addition for beta thalassemia
Authors
Keywords
-
Journal
ANNALS OF THE NEW YORK ACADEMY OF SCIENCES
Volume -, Issue -, Pages -
Publisher
Wiley
Online
2023-10-13
DOI
10.1111/nyas.15070
References
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- (2021) Franco Locatelli et al. NEW ENGLAND JOURNAL OF MEDICINE
- Northstar-3: Interim Results from a Phase 3 Study Evaluating Lentiglobin Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia and Either a β0 or IVS-I-110 Mutation at Both Alleles of the HBB Gene
- (2020) Ashutosh Lal et al. BLOOD
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- (2019) Sarah Marktel et al. NATURE MEDICINE
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- (2019) Agnieszka Czechowicz et al. Nature Communications
- Long-Term Clinical Outcomes of Lentiglobin Gene Therapy for Transfusion-Dependent β-Thalassemia in the Northstar (HGB-204) Study
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- (2010) Marina Cavazzana-Calvo et al. NATURE
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