Effect of ivacaftor in patients with advanced cystic fibrosis and a G551D-CFTR mutation: Safety and efficacy in an expanded access program in the United States

Title
Effect of ivacaftor in patients with advanced cystic fibrosis and a G551D-CFTR mutation: Safety and efficacy in an expanded access program in the United States
Authors
Keywords
Cystic fibrosis (CF), Cystic fibrosis transmembrane conductance regulator (CFTR), Lung function
Journal
Journal of Cystic Fibrosis
Volume 15, Issue 1, Pages 116-122
Publisher
Elsevier BV
Online
2015-02-11
DOI
10.1016/j.jcf.2015.01.008

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