In vivo topical gene therapy for recessive dystrophic epidermolysis bullosa: a phase 1 and 2 trial
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Title
In vivo topical gene therapy for recessive dystrophic epidermolysis bullosa: a phase 1 and 2 trial
Authors
Keywords
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Journal
NATURE MEDICINE
Volume 28, Issue 4, Pages 780-788
Publisher
Springer Science and Business Media LLC
Online
2022-03-29
DOI
10.1038/s41591-022-01737-y
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