Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy
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Title
Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy
Authors
Keywords
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Journal
JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION
Volume 327, Issue 15, Pages 1456
Publisher
American Medical Association (AMA)
Online
2022-04-06
DOI
10.1001/jama.2022.4315
References
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Note: Only part of the references are listed.- The Minimal Clinical Important Difference (MCID) in Annual Rate of Change of Timed Function Tests in Boys with DMD
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- Global epidemiology of Duchenne muscular dystrophy: an updated systematic review and meta-analysis
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- Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy
- (2020) Jerry R. Mendell et al. JAMA Neurology
- Therapeutic developments for Duchenne muscular dystrophy
- (2019) Ingrid E. C. Verhaart et al. Nature Reviews Neurology
- Normative data and percentile curves for the three-minute walk test and timed function tests in healthy Caucasian boys from 2.5 up to 6 years old
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- Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and neuromuscular, rehabilitation, endocrine, and gastrointestinal and nutritional management
- (2018) David J Birnkrant et al. LANCET NEUROLOGY
- Longitudinal effect of eteplirsen versus historical control on ambulation in Duchenne muscular dystrophy
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- (2016) Robert C. Griggs et al. NEUROLOGY
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- (2016) DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY
- Prednisone/prednisolone and deflazacort regimens in the CINRG Duchenne Natural History Study
- (2015) Luca Bello et al. NEUROLOGY
- Suitability of North Star Ambulatory Assessment in young boys with Duchenne muscular dystrophy
- (2015) Roberto De Sanctis et al. NEUROMUSCULAR DISORDERS
- Newborn bloodspot screening for Duchenne Muscular Dystrophy: 21 years experience in Wales (UK)
- (2013) Stuart J Moat et al. EUROPEAN JOURNAL OF HUMAN GENETICS
- Corticosteroids in Duchenne muscular dystrophy: Major variations in practice
- (2013) Robert C. Griggs et al. MUSCLE & NERVE
- Evidence-based path to newborn screening for duchenne muscular dystrophy
- (2012) Jerry R. Mendell et al. ANNALS OF NEUROLOGY
- Recommendations for the Primary Analysis of Continuous Endpoints in Longitudinal Clinical Trials
- (2012) Craig H. Mallinckrod† et al. DRUG INFORMATION JOURNAL
- Randomized, blinded trial of weekend vs daily prednisone in Duchenne muscular dystrophy
- (2011) D. M. Escolar et al. NEUROLOGY
- Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management
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- Diagnosis and management of Duchenne muscular dystrophy, part 2: implementation of multidisciplinary care
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- Reliability of the North Star Ambulatory Assessment in a multicentric setting
- (2009) E.S. Mazzone et al. NEUROMUSCULAR DISORDERS
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