Advances in the management of α-thalassemia major: reasons to be optimistic

Outcomes of allogeneic transplantation for hemoglobin Bart’s hydrops fetalis syndrome in Hong Kong

(2021) Wilson Y. K. Chan et al.   PEDIATRIC TRANSPLANTATION

Outcomes of haemoglobin Bart’s hydrops fetalis following intrauterine transfusion in Ontario, Canada

(2020) Hui Jue Zhang et al.   Archives of Disease in Childhood-Fetal and Neonatal Edition

Reduced Toxicity Conditioning for Nonmalignant Hematopoietic Cell Transplants

(2020) Cristina F. Contreras et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Fludarabine-based reduced toxicity yet myeloablative conditioning is effective and safe particularly in patients with high-risk thalassemia undergoing allogeneic transplantation

(2018) Vipul Sheth et al.   PEDIATRIC BLOOD & CANCER

Fetal stem cell and gene therapy

(2017) Russell Witt et al.   Seminars in Fetal & Neonatal Medicine

Complications of intrauterine intravascular blood transfusion: lessons learned after 1678 procedures

(2017) C. Zwiers et al.   ULTRASOUND IN OBSTETRICS & GYNECOLOGY

Successful matched unrelated donor stem cell transplant in Hemoglobin Bart's disease

(2016) M Y Elsaid et al.   BONE MARROW TRANSPLANTATION

Hemopoietic stem cell transplantation in thalassemia: a report from the European Society for Blood and Bone Marrow Transplantation Hemoglobinopathy Registry, 2000–2010

(2016) D Baronciani et al.   BONE MARROW TRANSPLANTATION

Non-genotoxic conditioning for hematopoietic stem cell transplantation using a hematopoietic-cell-specific internalizing immunotoxin

(2016) Rahul Palchaudhuri et al.   NATURE BIOTECHNOLOGY

Homozygous α-thalassemia: Challenges surrounding early identification, treatment, and cure

(2016) Lydia H. Pecker et al.   PEDIATRIC BLOOD & CANCER

Favorable outcomes afterin uterotransfusion in fetuses with alpha thalassemia major: a case series and review of the literature

(2016) Emily M. Kreger et al.   PRENATAL DIAGNOSIS

Society for Maternal-Fetal Medicine (SMFM) Clinical Guideline #8: The fetus at risk for anemia–diagnosis and management

(2015) Giancarlo Mari et al.   AMERICAN JOURNAL OF OBSTETRICS AND GYNECOLOGY

Correction of murine hemoglobinopathies by prenatal tolerance induction and postnatal nonmyeloablative allogeneic BM transplants

(2015) W. H. Peranteau et al.   BLOOD

Consensus statement from the first international conference for in utero stem cell transplantation and gene therapy

(2015) Tippi C. MacKenzie et al.   Frontiers in Pharmacology

Outcomes of Thalassemia Patients Undergoing Hematopoietic Stem Cell Transplantation by Using a Standard Myeloablative versus a Novel Reduced-Toxicity Conditioning Regimen According to a New Risk Stratification

(2014) Usanarat Anurathapan et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Mixed chimerism in haemoglobinopathies: from risk of graft rejection to immune tolerance

(2014) M. Andreani et al.   TISSUE ANTIGENS

Fludarabine and Exposure-Targeted Busulfan Compares Favorably with Busulfan/Cyclophosphamide-Based Regimens in Pediatric Hematopoietic Cell Transplantation: Maintaining Efficacy with Less Toxicity

(2013) I.H. Bartelink et al.   BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION

Normal cognitive functioning in a patient with Hb Bart’s hydrops successfully cured by hematopoietic SCT

(2013) B Pongtanakul et al.   BONE MARROW TRANSPLANTATION

Successful Unrelated Cord Blood Transplantation For Homozygous α-Thalassemia

(2013) Burak Gumuscu et al.   JOURNAL OF PEDIATRIC HEMATOLOGY ONCOLOGY

Birth prevalence of disorders detectable through newborn screening by race/ethnicity

(2012) Lisa Feuchtbaum et al.   GENETICS IN MEDICINE

Maternal T cells limit engraftment after in utero hematopoietic cell transplantation in mice

(2011) Amar Nijagal et al.   JOURNAL OF CLINICAL INVESTIGATION

Heterogeneity of Hemoglobin H Disease in Childhood

(2011) Ashutosh Lal et al.   NEW ENGLAND JOURNAL OF MEDICINE

High fludarabine exposure and relationship with treatment-related mortality after nonmyeloablative hematopoietic cell transplantation

(2010) J R Long-Boyle et al.   BONE MARROW TRANSPLANTATION

Homozygous α-Thalassemia Treated with Intrauterine Transfusions and Unrelated Donor Hematopoietic Cell Transplantation

(2009) Joanna S. Yi et al.   JOURNAL OF PEDIATRICS

Maternal Alloantigens Promote the Development of Tolerogenic Fetal Regulatory T Cells in Utero

(2008) J. E. Mold et al.   SCIENCE