Evaluation of the long-term treatment effects of intravenous idursulfase in patients with mucopolysaccharidosis II (MPS II) using statistical modeling: data from the Hunter Outcome Survey (HOS)
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Title
Evaluation of the long-term treatment effects of intravenous idursulfase in patients with mucopolysaccharidosis II (MPS II) using statistical modeling: data from the Hunter Outcome Survey (HOS)
Authors
Keywords
-
Journal
Orphanet Journal of Rare Diseases
Volume 16, Issue 1, Pages -
Publisher
Springer Science and Business Media LLC
Online
2021-10-30
DOI
10.1186/s13023-021-02052-4
References
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