Permanent inactivation of Huntington's disease mutation by personalized allele-specific CRISPR/Cas9
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Title
Permanent inactivation of Huntington's disease mutation by personalized allele-specific CRISPR/Cas9
Authors
Keywords
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Journal
HUMAN MOLECULAR GENETICS
Volume -, Issue -, Pages ddw286
Publisher
Oxford University Press (OUP)
Online
2016-09-16
DOI
10.1093/hmg/ddw286
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Related references
Note: Only part of the references are listed.- The HTT CAG-Expansion Mutation Determines Age at Death but Not Disease Duration in Huntington Disease
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- Sequence-Level Analysis of the Major European Huntington Disease Haplotype
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- (2012) Dongbo Yu et al. CELL
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