Alginate hydrogel polymers enable efficient delivery of a vascular-targeted AAV vector into aortic tissue

AAV-mediated TIMP-1 overexpression in aortic tissue reduces the severity of allograft vasculopathy in mice

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Subacute Liver Failure Following Gene Replacement Therapy for Spinal Muscular Atrophy Type I

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Gene transfer to the vascular system: Novel translational perspectives for vascular diseases

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From Clinical Trials to Clinical Practice: Practical Considerations for Gene Replacement Therapy in SMA Type 1

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Site-specific glycation and chemo-enzymatic antibody sortagging for the retargeting of rAAV6 to inflamed endothelium

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Immune Response Mechanisms against AAV Vectors in Animal Models

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Modulation of immune responses in lentiviral vector-mediated gene transfer

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Incorporation of Synthetic mRNA in Injectable Chitosan-Alginate Hybrid Hydrogels for Local and Sustained Expression of Exogenous Proteins in Cells

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Host Responses to Biomaterials and Anti-Inflammatory Design-a Brief Review

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Emerging Issues in AAV-Mediated In Vivo Gene Therapy

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Drug-Loadable Calcium Alginate Hydrogel System for Use in Oral Bone Tissue Repair

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Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65 -mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial

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A brain microvasculature endothelial cell‐specific viral vector with the potential to treat neurovascular and neurological diseases

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Specific gene delivery to liver sinusoidal and artery endothelial cells

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Isolation and culture of smooth muscle cells from human acute type A aortic dissection

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Endotoxins—the Invisible Companion in Biomaterials Research

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Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcripts

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Novel random peptide libraries displayed on AAV serotype 9 for selection of endothelial cell-directed gene transfer vectors

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Localized and Sustained Delivery of Silencing RNA from Macroscopic Biopolymer Hydrogels

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Cellular and molecular mechanisms of thoracic aortic aneurysms

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