AAV9-mediated gene transfer of desmin ameliorates cardiomyopathy in desmin-deficient mice

Rapid and highly efficient inducible cardiac gene knockout in adult mice using AAV-mediated expression of Cre recombinase

(2014) Stanislas Werfel et al.   CARDIOVASCULAR RESEARCH

Low dystrophin levels in heart can delay heart failure in mdx mice

(2014) Maaike van Putten et al.   JOURNAL OF MOLECULAR AND CELLULAR CARDIOLOGY

Mybpc3 gene therapy for neonatal cardiomyopathy enables long-term disease prevention in mice

(2014) Giulia Mearini et al.   Nature Communications

Recessive desmin-null muscular dystrophy with central nuclei and mitochondrial abnormalities

(2013) Matthew Henderson et al.   ACTA NEUROPATHOLOGICA

Desminopathies: pathology and mechanisms

(2012) Christoph S. Clemen et al.   ACTA NEUROPATHOLOGICA

Long-Term Preservation of Cardiac Structure and Function After Adeno-Associated Virus Serotype 9-Mediated Microdystrophin Gene Transfer in mdx Mice

(2012) Stefanie Schinkel et al.   HUMAN GENE THERAPY

Identification and characterization of two critical sequences in SV40PolyA that activate the green fluorescent protein reporter gene

(2011) Honggang Wang et al.   GENETICS AND MOLECULAR BIOLOGY

Desmin-related myopathy

(2010) KY van Spaendonck-Zwarts et al.   CLINICAL GENETICS

Intolerance to β-blockade in a mouse model of δ-sarcoglycan-deficient muscular dystrophy cardiomyopathy

(2010) Ralf Bauer et al.   EUROPEAN JOURNAL OF HEART FAILURE

Cardiac conduction disturbances and differential effects on atrial and ventricular electrophysiological properties in desmin deficient mice

(2010) Jan Wilko Schrickel et al.   JOURNAL OF INTERVENTIONAL CARDIAC ELECTROPHYSIOLOGY

Voluntary exercise induces structural remodeling in the hearts of dystrophin-deficient mice

(2010) Jeffrey M. Costas et al.   MUSCLE & NERVE

Prevention of cardiomyopathy in  -sarcoglycan knockout mice after systemic transfer of targeted adeno-associated viral vectors

(2009) C. Goehringer et al.   CARDIOVASCULAR RESEARCH

Tragedy in a heartbeat: malfunctioning desmin causes skeletal and cardiac muscle disease

(2009) Lev G. Goldfarb et al.   JOURNAL OF CLINICAL INVESTIGATION

Desmin-regulated Lentiviral Vectors for Skeletal Muscle Gene Transfer

(2009) Gillian E Talbot et al.   MOLECULAR THERAPY

Augmentation of AAV-mediated cardiac gene transfer after systemic administration in adult rats

(2008) O J Müller et al.   GENE THERAPY

Analysis of AAV Serotypes 1–9 Mediated Gene Expression and Tropism in Mice After Systemic Injection

(2008) Carmela Zincarelli et al.   MOLECULAR THERAPY