Towards access for all: 1st Working Group Report for the Global Gene Therapy Initiative (GGTI)

Biophysical and rheological biomarkers of red blood cell physiology and pathophysiology

(2021) Umut A. Gurkan   CURRENT OPINION IN HEMATOLOGY

Treating sickle cell anemia

(2020) John F. Tisdale et al.   SCIENCE

Whole blood viscosity and red blood cell adhesion: Potential biomarkers for targeted and curative therapies in sickle cell disease

(2020) Erdem Kucukal et al.   AMERICAN JOURNAL OF HEMATOLOGY

Automated Manufacture of Autologous CD19 CAR-T Cells for Treatment of Non-hodgkin Lymphoma

(2020) Zachary Jackson et al.   Frontiers in Immunology

Reduced HIV-1 latent reservoir outgrowth and distinct immune correlates among women in Rakai, Uganda

(2020) Jessica L. Prodger et al.   JCI Insight

Turning genes into medicines—what have we learned from gene therapy drug development in the past decade?

(2020) Katherine A. High   Nature Communications

Multi-stakeholder consensus on a target product profile for an HIV cure

(2020) Sharon R Lewin et al.   Lancet HIV

Sickle cell disease: Reducing the global disease burden

(2019) Joy Mburu et al.   International Journal of Laboratory Hematology

Multispecific anti-HIV duoCAR-T cells display broad in vitro antiviral activity and potent in vivo elimination of HIV-infected cells in a humanized mouse model

(2019) Kim Anthony-Gonda et al.   Science Translational Medicine

Development of a forward-oriented therapeutic lentiviral vector for hemoglobin disorders

(2019) Naoya Uchida et al.   Nature Communications

Applying the Behavioural and Social Sciences Research (BSSR) Functional Framework to HIV Cure Research

(2019) Karine Dubé et al.   Journal of the International AIDS Society

Gene therapy for sickle cell disease: An update

(2018) Selami Demirci et al.   CYTOTHERAPY

Clinical use of lentiviral vectors

(2018) Michael C. Milone et al.   LEUKEMIA

DNA engineered micromotors powered by metal nanoparticles for motion based cellphone diagnostics

(2018) Mohamed Shehata Draz et al.   Nature Communications

Sickle cell anemia in sub-Saharan Africa: advancing the clinical paradigm through partnerships and research

(2016) Patrick T. McGann et al.   BLOOD

Towards Multidisciplinary HIV-Cure Research: Integrating Social Science with Biomedical Research

(2016) Cynthia I. Grossman et al.   TRENDS IN MICROBIOLOGY

Improved Clinical Outcomes of High Risk β Thalassemia Major Patients Undergoing a HLA Matched Related Allogeneic Stem Cell Transplant with a Treosulfan Based Conditioning Regimen and Peripheral Blood Stem Cell Grafts

(2013) Vikram Mathews et al.   PLoS One

Global Burden of Sickle Cell Anaemia in Children under Five, 2010–2050: Modelling Based on Demographics, Excess Mortality, and Interventions

(2013) Frédéric B. Piel et al.   PLOS MEDICINE