Research priorities for rare neurological diseases: a representative view of patient representatives and healthcare professionals from the European Reference Network for Rare Neurological Diseases

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DNA repair pathways underlie a common genetic mechanism modulating onset in polyglutamine diseases

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A Systematic Review of Stakeholder Engagement in Comparative Effectiveness and Patient-Centered Outcomes Research

(2014) Thomas W. Concannon et al.   JOURNAL OF GENERAL INTERNAL MEDICINE

A Systematic Review of Approaches for Engaging Patients for Research on Rare Diseases

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Determining Research Priorities Through Partnership with Patients: An Overview

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Prevention and self-management interventions are top priorities for osteoarthritis systematic reviews

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