Correction of pathology in mice displaying Gaucher disease type 1 by a clinically-applicable lentiviral vector
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Title
Correction of pathology in mice displaying Gaucher disease type 1 by a clinically-applicable lentiviral vector
Authors
Keywords
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Journal
Molecular Therapy-Methods & Clinical Development
Volume 20, Issue -, Pages 312-323
Publisher
Elsevier BV
Online
2020-12-03
DOI
10.1016/j.omtm.2020.11.018
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