CRISPR/Cas9 mediated β-globin gene knockout in rabbits recapitulates human β-thalassemia

Hemopoietic stem cell transplantation in thalassemia: a report from the European Society for Blood and Bone Marrow Transplantation Hemoglobinopathy Registry, 2000–2010

(2016) D Baronciani et al.   BONE MARROW TRANSPLANTATION

KLF1-null neonates display hydrops fetalis and a deranged erythroid transcriptome

(2015) G. W. Magor et al.   BLOOD

Off-target Effects in CRISPR/Cas9-mediated Genome Engineering

(2015) Xiao-Hui Zhang et al.   Molecular Therapy-Nucleic Acids

Hypoxic Response Contributes to Altered Gene Expression and Precapillary Pulmonary Hypertension in Patients With Sickle Cell Disease

(2014) Xu Zhang et al.   CIRCULATION

Efficient RNA/Cas9-mediated genome editing in Xenopus tropicalis

(2014) X. Guo et al.   DEVELOPMENT

One-Step Generation of Mice Carrying Mutations in Multiple Genes by CRISPR/Cas-Mediated Genome Engineering

(2013) Haoyi Wang et al.   CELL

Generation of RAG 1- and 2-deficient rabbits by embryo microinjection of TALENs

(2013) Jun Song et al.   CELL RESEARCH

Genetic variation associated with circulating monocyte count in the eMERGE Network

(2013) David R. Crosslin et al.   HUMAN MOLECULAR GENETICS

High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells

(2013) Yanfang Fu et al.   NATURE BIOTECHNOLOGY

Transfusion complications in thalassemia patients: a report from the Centers for Disease Control and Prevention (CME)

(2013) Elliott Vichinsky et al.   TRANSFUSION

Spectrin Isoforms

(2011) Lucia R. Wolgast et al.   AMERICAN JOURNAL OF CLINICAL PATHOLOGY

Beta-thalassemia: from genotype to phenotype

(2011) F. Danjou et al.   HAEMATOLOGICA

Efficient Immunoglobulin Gene Disruption and Targeted Replacement in Rabbit Using Zinc Finger Nucleases

(2011) Tatiana Flisikowska et al.   PLoS One

Complications of thalassemia major and their treatment

(2011) Caterina Borgna-Pignatti et al.   Expert Review of Hematology

Tropomodulin 1-null mice have a mild spherocytic elliptocytosis with appearance of Tropomodulin 3 in red blood cells and disruption of the membrane skeleton

(2010) J. D. Moyer et al.   BLOOD

Beta-thalassemia

(2010) Antonio Cao et al.   GENETICS IN MEDICINE

Differential loss of embryonic globin genes during the radiation of placental mammals

(2008) J. C. Opazo et al.   PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA