Current and Future Treatment Approaches in Transthyretin Familial Amyloid Polyneuropathy
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Title
Current and Future Treatment Approaches in Transthyretin Familial Amyloid Polyneuropathy
Authors
Keywords
Transthyretin amyloidosis, Genetics, Treatment, Gene therapy, Tafamidis, Diflunisal
Journal
Current Treatment Options in Neurology
Volume 18, Issue 12, Pages -
Publisher
Springer Nature
Online
2016-11-21
DOI
10.1007/s11940-016-0436-z
References
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Note: Only part of the references are listed.- Novel conformation-specific monoclonal antibodies against amyloidogenic forms of transthyretin
- (2016) Jeffrey N. Higaki et al. AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
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- (2016) Yohei Misumi et al. LIVER TRANSPLANTATION
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- (2015) Yoshiki Sekijima et al. AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
- Liver transplantation in transthyretin amyloidosis: Issues and challenges
- (2015) Andreia Carvalho et al. LIVER TRANSPLANTATION
- Rapid progression of familial amyloidotic polyneuropathy
- (2015) David Adams et al. NEUROLOGY
- Therapeutic Clearance of Amyloid by Antibodies to Serum Amyloid P Component
- (2015) Duncan B. Richards et al. NEW ENGLAND JOURNAL OF MEDICINE
- Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study
- (2015) Ole B Suhr et al. Orphanet Journal of Rare Diseases
- Liver Transplantation for Hereditary Transthyretin Amyloidosis
- (2015) Bo-Göran Ericzon et al. TRANSPLANTATION
- Repurposing Diflunisal for Familial Amyloid Polyneuropathy
- (2015) John L. Berk et al. JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION
- CNS involvement in V30M transthyretin amyloidosis: clinical, neuropathological and biochemical findings
- (2014) L. F. Maia et al. JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY
- Efficacy of diflunisal on autonomic dysfunction of late-onset familial amyloid polyneuropathy (TTR Val30Met) in a Japanese endemic area
- (2014) Ryoichi Takahashi et al. JOURNAL OF THE NEUROLOGICAL SCIENCES
- Optimal combination secondary prevention drug treatment and stroke outcomes
- (2014) J.-H. Park et al. NEUROLOGY
- Effect on disability and safety of Tafamidis in late onset of Met30 transthyretin familial amyloid polyneuropathy
- (2013) P. Lozeron et al. EUROPEAN JOURNAL OF NEUROLOGY
- Neurophysiological markers of small fibre neuropathy in TTR-FAP mutation carriers
- (2013) Jean-Pascal Lefaucheur et al. JOURNAL OF NEUROLOGY
- Long-term effects of tafamidis for the treatment of transthyretin familial amyloid polyneuropathy
- (2013) Teresa Coelho et al. JOURNAL OF NEUROLOGY
- Changes in pathological and biochemical findings of systemic tissue sites in familial amyloid polyneuropathy more than 10 years after liver transplantation
- (2013) T. Oshima et al. JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY
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- (2013) Teresa Coelho et al. NEW ENGLAND JOURNAL OF MEDICINE
- Guideline of transthyretin-related hereditary amyloidosis for clinicians
- (2013) Yukio Ando et al. Orphanet Journal of Rare Diseases
- Effects of Tafamidis on Transthyretin Stabilization and Clinical Outcomes in Patients with Non-Val30Met Transthyretin Amyloidosis
- (2013) Giampaolo Merlini et al. Journal of Cardiovascular Translational Research
- Doxycycline plus tauroursodeoxycholic acid for transthyretin amyloidosis: a phase II study
- (2012) Laura Obici et al. AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
- Clinical development of an antisense therapy for the treatment of transthyretin-associated polyneuropathy
- (2012) Elizabeth J. Ackermann et al. AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
- The Transthyretin Amyloidosis Outcomes Survey (THAOS) registry: design and methodology
- (2012) Violaine Planté-Bordeneuve et al. CURRENT MEDICAL RESEARCH AND OPINION
- THAOS – The Transthyretin Amyloidosis Outcomes Survey: initial report on clinical manifestations in patients with hereditary and wild-type transthyretin amyloidosis
- (2012) Teresa Coelho et al. CURRENT MEDICAL RESEARCH AND OPINION
- Tafamidis for transthyretin familial amyloid polyneuropathy: A randomized, controlled trial
- (2012) T. Coelho et al. NEUROLOGY
- Long-term survival after liver transplantation in patients with familial amyloid polyneuropathy
- (2012) T. Yamashita et al. NEUROLOGY
- Tafamidis, a potent and selective transthyretin kinetic stabilizer that inhibits the amyloid cascade
- (2012) C. E. Bulawa et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Sustained pharmacological depletion of serum amyloid P component in patients with systemic amyloidosis
- (2010) Julian D. Gillmore et al. BRITISH JOURNAL OF HAEMATOLOGY
- Synergy of combined Doxycycline/TUDCA treatment in lowering Transthyretin deposition and associated biomarkers: studies in FAP mouse models
- (2010) Isabel Cardoso et al. Journal of Translational Medicine
- Risk of transmission of systemic transthyretin amyloidosis after domino liver transplantation
- (2010) Laura Lladó et al. LIVER TRANSPLANTATION
- Antibodies to human serum amyloid P component eliminate visceral amyloid deposits
- (2010) Karl Bodin et al. NATURE
- Progression of transthyretin amyloid neuropathy after liver transplantation
- (2010) J. J. Liepnieks et al. NEUROLOGY
- Lipid-like materials for low-dose, in vivo gene silencing
- (2010) K. T. Love et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Liver transplantation for familial amyloidotic polyneuropathy: Impact on Swedish patients' survival
- (2009) Sadahisa Okamoto et al. LIVER TRANSPLANTATION
- Heterogeneity of penetrance in familial amyloid polyneuropathy, ATTR Val30Met, in the Swedish population
- (2008) Urban Hellman et al. AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
- Neurophysiological markers in familial amyloid polyneuropathy patients: Early changes
- (2008) Isabel M. Conceição et al. CLINICAL NEUROPHYSIOLOGY
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