iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation

Title
iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation
Authors
Keywords
iPSC, Cystic Fibrosis, gene targeting, TALEN, intestinal organoids, FIS assay
Journal
Molecular Therapy-Methods & Clinical Development
Volume 17, Issue -, Pages 858-870
Publisher
Elsevier BV
Online
2020-04-18
DOI
10.1016/j.omtm.2020.04.005

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