Correction of amyotrophic lateral sclerosis related phenotypes in induced pluripotent stem cell-derived motor neurons carrying a hexanucleotide expansion mutation in C9orf72 by CRISPR/Cas9 genome editing using homology-directed repair
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Title
Correction of amyotrophic lateral sclerosis related phenotypes in induced pluripotent stem cell-derived motor neurons carrying a hexanucleotide expansion mutation in C9orf72 by CRISPR/Cas9 genome editing using homology-directed repair
Authors
Keywords
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Journal
HUMAN MOLECULAR GENETICS
Volume 29, Issue 13, Pages 2200-2217
Publisher
Oxford University Press (OUP)
Online
2020-06-01
DOI
10.1093/hmg/ddaa106
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