Treating Bietti crystalline dystrophy in a high-fat diet-exacerbated murine model using gene therapy
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Title
Treating Bietti crystalline dystrophy in a high-fat diet-exacerbated murine model using gene therapy
Authors
Keywords
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Journal
GENE THERAPY
Volume -, Issue -, Pages -
Publisher
Springer Science and Business Media LLC
Online
2020-06-02
DOI
10.1038/s41434-020-0159-3
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- Simultaneous generation and germline transmission of multiple gene mutations in rat using CRISPR-Cas systems
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