AAV5-miHTT Lowers Huntingtin mRNA and Protein without Off-Target Effects in Patient-Derived Neuronal Cultures and Astrocytes

Title
AAV5-miHTT Lowers Huntingtin mRNA and Protein without Off-Target Effects in Patient-Derived Neuronal Cultures and Astrocytes
Authors
Keywords
-
Journal
Molecular Therapy-Methods & Clinical Development
Volume 15, Issue -, Pages 275-284
Publisher
Elsevier BV
Online
2019-10-05
DOI
10.1016/j.omtm.2019.09.010

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