Long-Term Therapeutic Efficacy of Intravenous AAV-Mediated Hamartin Replacement in Mouse Model of Tuberous Sclerosis Type 1

Title
Long-Term Therapeutic Efficacy of Intravenous AAV-Mediated Hamartin Replacement in Mouse Model of Tuberous Sclerosis Type 1
Authors
Keywords
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Journal
Publisher
Elsevier BV
Online
2019-08-17
DOI
10.1016/j.omtm.2019.08.003

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