Translational studies of intravenous and intracerebroventricular routes of administration for CNS cellular biodistribution for BMN 250, an enzyme replacement therapy for the treatment of Sanfilippo type B
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Title
Translational studies of intravenous and intracerebroventricular routes of administration for CNS cellular biodistribution for BMN 250, an enzyme replacement therapy for the treatment of Sanfilippo type B
Authors
Keywords
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Journal
Drug Delivery and Translational Research
Volume -, Issue -, Pages -
Publisher
Springer Science and Business Media LLC
Online
2020-01-16
DOI
10.1007/s13346-019-00683-6
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