Generation of two compound heterozygous HGSNAT-mutated lines from healthy induced pluripotent stem cells using CRISPR/Cas9 to model Sanfilippo C syndrome

Title
Generation of two compound heterozygous HGSNAT-mutated lines from healthy induced pluripotent stem cells using CRISPR/Cas9 to model Sanfilippo C syndrome
Authors
Keywords
-
Journal
Stem Cell Research
Volume 41, Issue -, Pages 101616
Publisher
Elsevier BV
Online
2019-10-25
DOI
10.1016/j.scr.2019.101616

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