Early Outcome of a Phase I/II Clinical Trial (NCT03538899) of Gene-Corrected Autologous CD34+ Hematopoietic Cells and Low-Exposure Busulfan in Newly Diagnosed Patients with Artemis-Deficient Severe Combined Immunodeficiency (ART-SCID)

Title
Early Outcome of a Phase I/II Clinical Trial (NCT03538899) of Gene-Corrected Autologous CD34+ Hematopoietic Cells and Low-Exposure Busulfan in Newly Diagnosed Patients with Artemis-Deficient Severe Combined Immunodeficiency (ART-SCID)
Authors
Keywords
-
Journal
BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION
Volume 26, Issue 3, Pages S88-S89
Publisher
Elsevier BV
Online
2020-01-24
DOI
10.1016/j.bbmt.2019.12.589

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