In Vivo Gene Therapy for Mucopolysaccharidosis Type III (Sanfilippo Syndrome): A New Treatment Horizon

Title
In Vivo Gene Therapy for Mucopolysaccharidosis Type III (Sanfilippo Syndrome): A New Treatment Horizon
Authors
Keywords
-
Journal
HUMAN GENE THERAPY
Volume 30, Issue 10, Pages 1211-1221
Publisher
Mary Ann Liebert Inc
Online
2019-09-04
DOI
10.1089/hum.2019.217

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