Erythrocyte Encapsulated Thymidine Phosphorylase for the Treatment of Patients with Mitochondrial Neurogastrointestinal Encephalomyopathy: Study Protocol for a Multi-Centre, Multiple Dose, Open Label Trial

Safety and Efficacy of Erythrocyte Encapsulated Thymidine Phosphorylase in Mitochondrial Neurogastrointestinal Encephalomyopathy

(2019) Michelle Levene et al.   Journal of Clinical Medicine

Liver transplant reverses biochemical imbalance in mitochondrial neurogastrointestinal encephalomyopathy

(2017) Roberto D'Angelo et al.   MITOCHONDRION

Liver transplantation for mitochondrial neurogastrointestinal encephalomyopathy

(2016) Roberto De Giorgio et al.   ANNALS OF NEUROLOGY

Allogeneic haematopoietic stem cell transplantation for mitochondrial neurogastrointestinal encephalomyopathy

(2015) Joerg P. Halter et al.   BRAIN

Development of the NIH Patient-Reported Outcomes Measurement Information System (PROMIS) Gastrointestinal Symptom Scales

(2014) Brennan M R Spiegel et al.   AMERICAN JOURNAL OF GASTROENTEROLOGY

SPIRIT 2013 Statement: Defining Standard Protocol Items for Clinical Trials

(2013) An-Wen Chan et al.   ANNALS OF INTERNAL MEDICINE

Clinical and biochemical improvements in a patient with MNGIE following enzyme replacement

(2013) B. E. Bax et al.   NEUROLOGY

Psychosocial Effects of Cancer Cachexia: A Systematic Literature Search and Qualitative Analysis

(2012) Rolf Oberholzer et al.   JOURNAL OF PAIN AND SYMPTOM MANAGEMENT

Clinical and genetic spectrum of mitochondrial neurogastrointestinal encephalomyopathy

(2011) Caterina Garone et al.   BRAIN

Allogeneic hematopoietic SCT as treatment option for patients with mitochondrial neurogastrointestinal encephalomyopathy (MNGIE): a consensus conference proposal for a standardized approach

(2010) J Halter et al.   BONE MARROW TRANSPLANTATION

Gastrointestinal Dysmotility in Mitochondrial Neurogastrointestinal Encephalomyopathy Is Caused by Mitochondrial DNA Depletion

(2008) Carla Giordano et al.   AMERICAN JOURNAL OF PATHOLOGY

CARRIER ERYTHROCYTE ENTRAPPED THYMIDINE PHOSPHORYLASE THERAPY FOR MNGIE

(2008) N. F. Moran et al.   NEUROLOGY