Bezafibrate Enhances AAV Vector-Mediated Genome Editing in Glycogen Storage Disease Type Ia

Published 2019 View Full Article

Authors

Keywords

glycogen storage disease type Ia, adeno-associated virus, bezafibrate, gene therapy, genome editing, zinc-finger nuclease, pan-agonist of peroxisome proliferator-activated receptors, autophagy

Journal

Molecular Therapy-Methods & Clinical Development

Volume 13, Issue -, Pages 265-273

Publisher

Elsevier BV

Online

2019-02-11

DOI

10.1016/j.omtm.2019.02.002

Ask authors/readers for more resources

Protocol

Community support

Reagent

Community support

Reprint

Contact the author

Become a Peeref-certified reviewer

The Peeref Institute provides free reviewer training that teaches the core competencies of the academic peer review process.

Get Started

Ask a Question. Answer a Question.

Quickly pose questions to the entire community. Debate answers and get clarity on the most important issues facing researchers.

Get Started